Division of Nephrology, Department of Medicine, Washington University School of Medicine, St. Louis, MO.
Maternal Fetal Medicine, San Gabriel Valley Perinatal Medical Group, Pomona Valley Hospital Medical Center, Pomona, CA.
Adv Kidney Dis Health. 2024 May;31(3):255-264. doi: 10.1053/j.akdh.2023.09.003.
Thrombotic microangiopathy (TMA) is a pathological lesion that occurs due to endothelial injury. It can be seen in a heterogenous group of disorders, typically characterized by microangiopathic hemolytic anemia, thrombocytopenia, and end-organ ischemia. TMA can also be renal limited with no systemic manifestations. There are multiple etiologies of a TMA with complement activation being a core underlying mechanism, although the nature and extent of complement involvement can vary. A further complicated factor is the cross talk between complement, neutrophils, and coagulation pathways in the pathophysiology of TMAs. Therefore, a thorough and systematic clinical history and laboratory evaluation are critical to establish the cause and pathophysiology of a TMA. Furthermore, TMAs are associated with significant morbidity and mortality, and timely diagnosis is key for appropriate management and to prevent end-stage kidney disease and other associated complications. In this review, we focus on the pathology, mechanisms, diagnostic work up and treatment of TMAs associated with various etiologies. We also define the complement evaluations that should be conducted in these patients and further highlight the currently approved complement therapies as well as others in the pipeline.
血栓性微血管病(TMA)是一种由于内皮细胞损伤而发生的病理病变。它可以在一组异质的疾病中看到,通常表现为微血管性溶血性贫血、血小板减少和终末器官缺血。TMA 也可以局限于肾脏而无全身表现。TMA 有多种病因,补体激活是其核心潜在机制,尽管补体的性质和程度的参与可能有所不同。另一个复杂的因素是补体、中性粒细胞和凝血途径在 TMA 病理生理学中的相互作用。因此,彻底和系统的临床病史和实验室评估对于确定 TMA 的病因和发病机制至关重要。此外,TMA 与显著的发病率和死亡率相关,及时诊断是适当管理和预防终末期肾病和其他相关并发症的关键。在这篇综述中,我们重点介绍了与各种病因相关的 TMA 的病理学、机制、诊断和治疗。我们还定义了应在这些患者中进行的补体评估,并进一步强调了目前批准的补体治疗方法以及其他正在研发中的方法。