Neurocognitive assessment platform for clinical trials in PKU: White paper developed by the NPKUA neurocognitive workgroup.
作者信息
Waisbren Susan E, Christ Shawn E, Bilder Deborah A, Bjoraker Kendra J, Bolton Scout, Chamberlin Sarah, Grant Mitzie L, Janzen Darren M, Katz Rachel, Lubliner Eugene, Martin Arianna, McQueen Kelsey, Moshkovich Olga, Nguyen-Driver Mina, Shim Soo, Stefanatos Arianna K, Wilkening Greta, Harding Cary
机构信息
Boston Children's Hospital and Harvard Medical School, Boston, MA, United States of America.
Clinical Neuropsychology Laboratory, University of Missouri, Columbia, MO, United States of America.
出版信息
Mol Genet Metab. 2024 Sep-Oct;143(1-2):108555. doi: 10.1016/j.ymgme.2024.108555. Epub 2024 Jul 25.
Abstract
摘要
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