York Health Economics Consortium, University of York, York, United Kingdom.
University Hospitals of Coventry and Warwickshire, Department of Neurosciences, University of Warwick, Coventry, United Kingdom.
J Neurol Sci. 2024 Sep 15;464:123172. doi: 10.1016/j.jns.2024.123172. Epub 2024 Aug 6.
Highly active (HA) relapsing remitting multiple sclerosis (RRMS) is associated with frequent relapses and high burden of disease/disability. Natalizumab is licensed for HA RRMS, including rapidly evolving severe (RES) (≥2 relapses in previous year) and sub-optimally treated (SOT) (≥1 relapse in previous year despite treatment) populations. However, there is limited RCT evidence in the SOT subpopulation.
To review the non-RCT evidence for natalizumab in SOT HA RRMS.
Databases were searched to January 2023 for non-randomised studies of natalizumab in HA RRMS. Studies in patients with ≥1 relapse during previous treatment were eligible for inclusion. Meta-analyses were conducted to compare natalizumab with platform and higher efficacy disease-modifying therapies, with sensitivity analysis restricted to studies of low risk of bias.
Included comparative studies (n = 16) showed natalizumab had lower relapse rates, disease activity and MRI (radiological) outcomes compared with platform and higher efficacy therapy. Case series (n = 11) showed natalizumab was associated with high rates of freedom from relapse and clinical/radiological disease activity and reductions in annualised relapse rate and disability progression.
Literature reviewed indicates that natalizumab is more effective than other included treatments for SOT patients. Findings were consistent with studies in the broad HA RRMS population, suggesting that natalizumab may have similar efficacy for SOT and RES HA RRMS.
高疾病活动度(HA)复发缓解型多发性硬化症(RRMS)与频繁复发和高疾病负担/残疾有关。那他珠单抗被批准用于 HA RRMS,包括快速进展性严重型(RES)(前一年发生≥2 次复发)和治疗效果欠佳型(SOT)(前一年发生≥1 次复发但仍在接受治疗)患者。然而,SOT 亚组人群的 RCT 证据有限。
综述那他珠单抗治疗 SOT HA RRMS 的非 RCT 证据。
检索截至 2023 年 1 月的数据库,以寻找 HA RRMS 中那他珠单抗的非随机对照研究。纳入在前次治疗期间发生≥1 次复发的患者的研究。对那他珠单抗与平台和高疗效疾病修正疗法进行了荟萃分析,并对低偏倚风险的研究进行了敏感性分析。
纳入的对照研究(n=16)表明,与平台和高疗效治疗相比,那他珠单抗的复发率、疾病活动度和 MRI(放射学)结局更低。病例系列研究(n=11)表明,那他珠单抗与较高的无复发率以及临床/放射学疾病活动度相关,同时降低了年复发率和残疾进展率。
综述文献表明,那他珠单抗比其他纳入的治疗方法对 SOT 患者更有效。这些发现与广泛的 HA RRMS 人群中的研究一致,表明那他珠单抗对 SOT 和 RES HA RRMS 可能具有相似的疗效。