Cell Biology, Neurobiology and Biophysics, Department of Biology, Faculty of Science, Utrecht University, Utrecht, Netherlands.
Department of Cell Biology, University Medical Center Groningen, University of Groningen, Groningen, Netherlands.
J Cell Biol. 2024 Nov 4;223(11). doi: 10.1083/jcb.202307142. Epub 2024 Aug 16.
Huntington's disease (HD) is caused by a polyglutamine expansion of the huntingtin protein, resulting in the formation of polyglutamine aggregates. The mechanisms of toxicity that result in the complex HD pathology remain only partially understood. Here, we show that nuclear polyglutamine aggregates induce nuclear envelope (NE) blebbing and ruptures that are often repaired incompletely. These ruptures coincide with disruptions of the nuclear lamina and lead to lamina scar formation. Expansion microscopy enabled resolving the ultrastructure of nuclear aggregates and revealed polyglutamine fibrils sticking into the cytosol at rupture sites, suggesting a mechanism for incomplete repair. Furthermore, we found that NE repair factors often accumulated near nuclear aggregates, consistent with stalled repair. These findings implicate nuclear polyQ aggregate-induced loss of NE integrity as a potential contributing factor to Huntington's disease and other polyglutamine diseases.
亨廷顿病(HD)是由亨廷顿蛋白的多聚谷氨酰胺扩展引起的,导致多聚谷氨酰胺聚集的形成。导致复杂的 HD 病理学的毒性机制仍仅部分理解。在这里,我们表明核多聚谷氨酰胺聚集诱导核膜(NE)泡状和破裂,这些破裂通常不完全修复。这些破裂与核纤层的破坏一致,并导致核纤层瘢痕形成。扩展显微镜使能够解析核聚集体的超微结构,并显示出在破裂部位突入细胞质的聚谷氨酰胺纤维,提示了不完全修复的机制。此外,我们发现 NE 修复因子经常在核聚集体附近积累,这与修复停滞一致。这些发现表明核多聚 Q 聚集诱导的 NE 完整性丧失可能是亨廷顿病和其他多聚谷氨酰胺疾病的一个潜在致病因素。