Division of Endocrinology, Diabetes and Metabolism, Department of Medicine, University of Pittsburgh, Pittsburgh, Pennsylvania, USA.
Department of Pathology, University of Pittsburgh, Pittsburgh, Pennsylvania, USA.
Endocr Relat Cancer. 2024 Nov 22;31(12). doi: 10.1530/ERC-24-0207. Print 2024 Dec 1.
BRAFK601E is an uncommon mutation typically found in encapsulated follicular-patterned thyroid tumors. Previous studies on BRAFK601E-positive thyroid tumors were conducted before the implementation of the non-invasive follicular neoplasm with papillary-like nuclear features (NIFTP) diagnosis. This study aimed to characterize BRAFK601E-positive tumors and evaluate changes in the diagnosis and management of these patients after the introduction of NIFTP. We evaluated 25 thyroid tumors that were positive for BRAFK601E and diagnosed considering the NIFTP criteria. Clinicopathologic characteristics and recurrence rates of these tumors were compared to 29 BRAFK601E-positive tumors diagnosed prior to the acceptance of the NIFTP diagnosis. RNA-seq analysis was performed on 10 BRAFK601E-positive tumors. In the current study, 72% of BRAFK601E-positive tumors were diagnosed as non-invasive tumors on resection, with NIFTP (48% of all tumors) being the most common diagnosis. BRAFK601E-positive tumors exhibited a RAS-like gene expression profile with a BRAF-RAS score (BRS) and thyroid differentiation score (TDS) distinct from BRAFV600E-positive tumors (P < 0.001). Since 2016, patients with BRAFK601E-positive tumors less frequently underwent total thyroidectomy (41% vs 100%, P < 0.001) and received radioiodine (7% vs 75%, P < 0.001). None of the tumors positive for an isolated BRAFK601E mutation from the current or 2016 studies showed recurrences on follow-up. Our study demonstrates that most BRAFK601E-positive tumors are low-risk, RAS-like tumors, which were diagnosed as NIFTP in half of all study cases. Since 2016, patients with BRAFK601E-positive nodules have received less aggressive treatment. The risk of recurrence of BRAFK601E-positive tumors without other high-risk features appears to be low, and lobectomy without radioiodine is likely a sufficient treatment for these patients.
BRAFK601E 是一种不常见的突变,通常在包裹滤泡模式的甲状腺肿瘤中发现。以前对 BRAFK601E 阳性甲状腺肿瘤的研究是在非浸润性滤泡性肿瘤伴乳头状核特征(NIFTP)诊断实施之前进行的。本研究旨在描述 BRAFK601E 阳性肿瘤,并评估在引入 NIFTP 后这些患者的诊断和治疗变化。我们评估了 25 例 BRAFK601E 阳性且符合 NIFTP 标准的甲状腺肿瘤。比较了这些肿瘤的临床病理特征和复发率与 29 例在接受 NIFTP 诊断之前诊断为 BRAFK601E 阳性的肿瘤。对 10 例 BRAFK601E 阳性肿瘤进行了 RNA-seq 分析。在本研究中,72%的 BRAFK601E 阳性肿瘤在切除时被诊断为非浸润性肿瘤,其中 NIFTP(所有肿瘤的 48%)是最常见的诊断。BRAFK601E 阳性肿瘤表现出类似于 RAS 的基因表达谱,具有 BRAF-RAS 评分(BRS)和甲状腺分化评分(TDS)与 BRAFV600E 阳性肿瘤不同(P < 0.001)。自 2016 年以来,BRAFK601E 阳性肿瘤患者较少接受甲状腺全切除术(41%对 100%,P < 0.001)和放射性碘治疗(7%对 75%,P < 0.001)。在当前或 2016 年的研究中,没有一例仅存在 BRAFK601E 突变的肿瘤在随访中复发。本研究表明,大多数 BRAFK601E 阳性肿瘤是低风险、类似于 RAS 的肿瘤,在所有研究病例中一半被诊断为 NIFTP。自 2016 年以来,BRAFK601E 阳性结节患者接受了侵袭性较小的治疗。没有其他高危特征的 BRAFK601E 阳性肿瘤的复发风险似乎较低,对于这些患者,行腺叶切除术而不进行放射性碘治疗可能是一种足够的治疗方法。