Daley Brianna R, Sealover Nancy E, Finniff Bridget A, Hughes Jacob M, Sheffels Erin, Gerlach Daniel, Hofmann Marco H, Kostyrko Kaja, LaMorte Joseph P, Linke Amanda J, Beckley Zaria, Frank Andrew M, Lewis Robert E, Wilkerson Matthew D, Dalgard Clifton L, Kortum Robert L
Department of Pharmacology and Molecular Therapeutics, Uniformed Services University of the Health Sciences, Bethesda, Maryland.
USU Physician-Scientist Training Program, Uniformed Services University of the Health Sciences, Bethesda, Maryland.
Cancer Res. 2025 Jan 2;85(1):118-133. doi: 10.1158/0008-5472.CAN-23-3256.
The clinical effectiveness of KRASG12C inhibitors (G12Ci) is limited both by intrinsic and acquired resistance, necessitating the development of combination approaches. Here, we identified targeting proximal receptor tyrosine kinase signaling using the SOS1 inhibitor (SOS1i) BI-3406 as a strategy to improve responses to G12Ci treatment. SOS1i enhanced the efficacy of G12Ci and limited rebound receptor tyrosine kinase/ERK signaling to overcome intrinsic/adaptive resistance, but this effect was modulated by SOS2 protein levels. G12Ci drug-tolerant persister (DTP) cells showed up to a 3-fold enrichment of tumor-initiating cells (TIC), suggestive of a sanctuary population of G12Ci-resistant cells. SOS1i resensitized DTPs to G12Ci and inhibited G12C-induced TIC enrichment. Co-mutation of the tumor suppressor KEAP1 limited the clinical effectiveness of G12Ci, and KEAP1 and STK11 deletion increased TIC frequency and accelerated the development of acquired resistance to G12Ci, consistent with clinical G12Ci resistance seen with these co-mutations. Treatment with SOS1i both delayed acquired G12Ci resistance and limited the total number of resistant colonies regardless of KEAP1 and STK11 mutational status. Together, these data suggest that targeting SOS1 could be an effective strategy to both enhance G12Ci efficacy and prevent G12Ci resistance regardless of co-mutations. Significance: The SOS1 inhibitor BI-3406 both inhibits intrinsic/adaptive resistance and targets drug tolerant persister cells to limit the development of acquired resistance to clinical KRASG12C inhibitors in lung adenocarcinoma cells.
KRASG12C抑制剂(G12Ci)的临床疗效受到内在抗性和获得性抗性的限制,因此需要开发联合治疗方法。在此,我们确定了使用SOS1抑制剂(SOS1i)BI-3406靶向近端受体酪氨酸激酶信号传导,作为提高对G12Ci治疗反应的策略。SOS1i增强了G12Ci的疗效,并限制了受体酪氨酸激酶/ERK信号的反弹,以克服内在/适应性抗性,但这种作用受SOS2蛋白水平的调节。G12Ci药物耐受性持久性(DTP)细胞显示肿瘤起始细胞(TIC)富集高达3倍,提示存在G12Ci抗性细胞的避难所群体。SOS1i使DTP对G12Ci重新敏感,并抑制G12C诱导的TIC富集。肿瘤抑制因子KEAP1的共突变限制了G12Ci的临床疗效,KEAP1和STK11缺失增加了TIC频率,并加速了对G12Ci获得性抗性的发展,这与这些共突变在临床上观察到的G12Ci抗性一致。无论KEAP1和STK11的突变状态如何,用SOS1i治疗既能延缓G12Ci获得性抗性的发生,又能限制抗性克隆的总数。总之,这些数据表明,靶向SOS1可能是一种有效的策略,既能增强G12Ci的疗效,又能预防G12Ci抗性,而不受共突变的影响。意义:SOS1抑制剂BI-3406既能抑制内在/适应性抗性,又能靶向药物耐受性持久性细胞,以限制肺腺癌细胞对临床KRASG12C抑制剂获得性抗性的发展。