When promising therapies are out of reach: Ethical responsibilities of stakeholders in gene therapy trials for rare disorders.
作者信息
Major Rami M, Yavarow Zollie
机构信息
Department of Social Medicine and Center for Bioethics, University of North Carolina at Chapel Hill, Chapel Hill, NC, USA; Curriculum in Genetics and Molecular Biology, University of North Carolina at Chapel Hill, Chapel Hill, NC, USA.
Cure VCP Disease, Warner Robins, GA, USA.
出版信息
Mol Ther. 2025 Jan 8;33(1):30-31. doi: 10.1016/j.ymthe.2024.11.019. Epub 2024 Nov 28.
Abstract
摘要
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