Second gene therapy for hemophilia B approved: More answers or questions?
作者信息
Kaczmarek Radoslaw, Pierce Glenn F
机构信息
Department of Pediatrics, Indiana University School of Medicine, Indianapolis, IN, USA.
World Federation of Hemophilia, Montreal, QC, Canada.
出版信息
Mol Ther. 2025 Jan 8;33(1):1-2. doi: 10.1016/j.ymthe.2024.11.026. Epub 2024 Nov 29.
Abstract
摘要
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