Reddy Siddhartha Thammineni, Hosoya Hitomi, Mikkilineni Lekha
Division of Bone and Marrow Transplantation & Cellular Therapies, Stanford University, 870 Welch Road, Palo Alto, CA, 94304, USA.
Hackensack University Medical Center, NJ, USA.
Cancer Metastasis Rev. 2024 Dec 3;44(1):14. doi: 10.1007/s10555-024-10219-1.
Chimeric antigen receptor (CAR) T-cell therapy represents a transformative advancement in treating relapsed or refractory multiple myeloma (MM) in both early- and late-line settings. MM, a plasma cell malignancy, traditionally requires ongoing complex drug regimens, posing significant burdens on patients. In contrast, CAR T-cell therapy offers a one-time treatment option without the need for continuous maintenance therapy. CAR T-cell therapy leverages engineered T-cells to target specific antigens on tumor cells, leading to their elimination. Current approved therapies target B-cell maturation antigen (BCMA); new targets are under investigation, such as G-protein-coupled receptor class C group 5 member D (GPRC5D). Despite its efficacy, CAR T-cell therapy is associated with serious toxicities such as cytokine release syndrome (CRS) and immune-effector cell-associated neurotoxicity syndrome (ICANS), necessitating careful management. The review will provide an overview of the design and manufacturing of CAR T-cells and current FDA indications, as well as challenges and future directions of CAR-T therapy for MM treatment.
嵌合抗原受体(CAR)T细胞疗法是治疗复发或难治性多发性骨髓瘤(MM)在一线和多线治疗中的一项变革性进展。MM是一种浆细胞恶性肿瘤,传统上需要持续进行复杂的药物治疗方案,给患者带来巨大负担。相比之下,CAR T细胞疗法提供了一种一次性治疗选择,无需持续维持治疗。CAR T细胞疗法利用经过工程改造的T细胞靶向肿瘤细胞上的特定抗原,从而导致肿瘤细胞被清除。目前获批的疗法靶向B细胞成熟抗原(BCMA);新的靶点正在研究中,如G蛋白偶联受体C类第5组成员D(GPRC5D)。尽管CAR T细胞疗法有效,但它与细胞因子释放综合征(CRS)和免疫效应细胞相关神经毒性综合征(ICANS)等严重毒性相关,需要谨慎管理。本综述将概述CAR T细胞的设计和制造、目前美国食品药品监督管理局(FDA)的适应症,以及CAR-T疗法治疗MM的挑战和未来方向。