Butterfield Sienna P, Sizer Rebecca E, Saunders Fay L, White Robert J
Department of Biology, University of York, York, UK.
FUJIFILM Diosynth Biotechnologies, Billingham, UK.
Biotechnol J. 2024 Dec;19(12):e202400474. doi: 10.1002/biot.202400474.
Industrial production of biologics typically involves the integration of transgenes into host cell genomes, most often Chinese hamster ovary (CHO) cells. Epigenetic control of transgene expression is a major determinant of production titers. Although the cytomegalovirus (CMV) promoter has long been used to drive industrial transgene expression, we found that its associated histones are suboptimally acetylated in CHO cells, providing an opportunity to enhance productivity through epigenetic manipulation. Expression of monoclonal antibody mRNAs increased up to 12-fold when a CRISPR-dCas9 system delivered the catalytic domain of a histone acetyltransferase to the CMV promoter. This effect was far stronger than when promoter DNA was selectively demethylated using dCas9 fused to a 5-methylcytosine dioxygenase. Mechanistically, acetylation-mediated transcriptional activation involved heightened phosphorylation and activity of RNA polymerase II, enabling it to escape promoter-proximal pausing at the transgene. This approach almost doubled the titer and specific productivity of antibody-producing CHO cells, demonstrating the potential for biomanufacturing.
生物制品的工业化生产通常涉及将转基因整合到宿主细胞基因组中,最常见的是中国仓鼠卵巢(CHO)细胞。转基因表达的表观遗传控制是生产滴度的主要决定因素。尽管长期以来巨细胞病毒(CMV)启动子一直用于驱动工业转基因表达,但我们发现其相关组蛋白在CHO细胞中的乙酰化程度未达最佳状态,这为通过表观遗传操作提高生产力提供了契机。当CRISPR-dCas9系统将组蛋白乙酰转移酶的催化结构域传递至CMV启动子时,单克隆抗体mRNA的表达增加了12倍。这种效应远强于使用与5-甲基胞嘧啶双加氧酶融合的dCas9对启动子DNA进行选择性去甲基化时的效果。从机制上讲,乙酰化介导的转录激活涉及RNA聚合酶II磷酸化增强及活性提高,使其能够逃离转基因处启动子近端的暂停状态。这种方法使产生抗体的CHO细胞的滴度和比生产力几乎提高了一倍,证明了其在生物制造方面的潜力。