CRISPR/Cas13d targeting suppresses repeat-associated non-AUG translation of C9orf72 hexanucleotide repeat RNA.
作者信息
Liu Honghe, Zhao Xiao-Feng, Lu Yu-Ning, Hayes Lindsey R, Wang Jiou
出版信息
J Clin Invest. 2024 Dec 16;134(24):e189439. doi: 10.1172/JCI189439.
Abstract
摘要
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