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Thrombotic thrombocytopenic purpura with juvenile systemic lupus erythematosus: successful treatment with caplacizumab and rituximab.

作者信息

Yokoyama Tadafumi, Mimura Takuya, Tanaka Hiroki, Kasahara Ria, Usami Masaaki, Matsuda Yusuke, Fujiki Toshihiro, Wada Taizo

机构信息

Department of Pediatrics, Kanazawa University Hospital, Takara-machi 13-1, Kanazawa, 920-8640, Ishikawa, Japan.

Department of Pediatrics, National Hospital Organization, Kanazawa Medical Center, Shimoishiibiki-machi 1-1, Kanazawa, 920-8650, Ishikawa, Japan.

出版信息

Pediatr Rheumatol Online J. 2024 Dec 18;22(1):106. doi: 10.1186/s12969-024-01049-0.

DOI:10.1186/s12969-024-01049-0
PMID:39696445
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC11654370/
Abstract
摘要
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/25e2/11654370/8aa8cf947329/12969_2024_1049_Fig2_HTML.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/25e2/11654370/f442d2b247eb/12969_2024_1049_Fig1_HTML.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/25e2/11654370/8aa8cf947329/12969_2024_1049_Fig2_HTML.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/25e2/11654370/f442d2b247eb/12969_2024_1049_Fig1_HTML.jpg
https://cdn.ncbi.nlm.nih.gov/pmc/blobs/25e2/11654370/8aa8cf947329/12969_2024_1049_Fig2_HTML.jpg

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本文引用的文献

1
Effectiveness and safety of B cell-targeting biologics in the treatment of lupus nephritis: a systematic review and network meta‑analysis.B 细胞靶向生物制剂治疗狼疮肾炎的疗效和安全性:系统评价和网络荟萃分析。
Ren Fail. 2024 Dec;46(2):2416605. doi: 10.1080/0886022X.2024.2416605. Epub 2024 Oct 23.
2
Caplacizumab in pediatric immune thrombotic thrombocytopenic purpura: the UK TTP Registry experience.卡普拉西单抗在儿科免疫性血栓性血小板减少性紫癜中的应用:英国 TTP 登记处经验。
Blood Adv. 2024 Sep 10;8(17):4563-4567. doi: 10.1182/bloodadvances.2024013488.
3
Caplacizumab Treatment for Acquired Thrombotic Thrombocytopenic Purpura.
卡普拉珠单抗治疗获得性血栓性血小板减少性紫癜。
N Engl J Med. 2019 Jan 24;380(4):335-346. doi: 10.1056/NEJMoa1806311. Epub 2019 Jan 9.
4
Thrombotic thrombocytopenic purpura.血栓性血小板减少性紫癜。
Blood. 2017 May 25;129(21):2836-2846. doi: 10.1182/blood-2016-10-709857. Epub 2017 Apr 17.
5
Caplacizumab for Acquired Thrombotic Thrombocytopenic Purpura.卡普雷珠单抗治疗获得性血栓性血小板减少性紫癜。
N Engl J Med. 2016 Feb 11;374(6):511-22. doi: 10.1056/NEJMoa1505533.