2025年的镰状细胞贫血治疗
Sickle cell anaemia therapy in 2025.
作者信息
Schechter Alan N
机构信息
Molecular Medicine Branch, National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, Maryland, USA.
出版信息
Br J Haematol. 2025 Mar;206(3):842-845. doi: 10.1111/bjh.19933. Epub 2024 Dec 22.
Abstract
New pharmacological therapies for sickle cell anaemia have not been as efficacious as hoped, while widespread application of curative stem cell and gene therapies is not likely to occur soon. This situation raises the question about whether more attention now be devoted to the use of hydroxyurea in this disease.
摘要
镰状细胞贫血的新药理疗法并未达到预期效果，而治愈性干细胞和基因疗法的广泛应用近期也不太可能实现。这种情况引发了一个问题，即现在是否应更多关注羟基脲在该疾病中的应用。
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