Koo Jain, Shin Yuseon, Jeon Hyewon, Cheong Jaehyun, Cho Seongmin, Park Chanho, Song Ee Chan, Ramsey Jacob D, Lim Chaemin, Oh Kyung Taek
Department of Global Innovative Drugs, The Graduate School of Chung-Ang University, 221 Heukseok-dong, Dongjak-gu, Seoul 06974, Republic of Korea; College of Pharmacy, Chung-Ang University, 221 Heukseok-dong, Dongjak-gu, Seoul 06974, Republic of Korea.
Remedi Co., Ltd. Research center, Songdo 21990, Republic of Korea.
J Control Release. 2025 Feb 10;378:997-1012. doi: 10.1016/j.jconrel.2024.12.058. Epub 2025 Jan 2.
Glioblastoma multiforme (GBM) is a devastating primary tumor of the central nervous system with a significantly poor prognosis. The primary challenge in treating GBM lies in the restrictive nature of the blood-brain barrier (BBB), impeding effective drug delivery to the brain. In this study, intranasal polymeric micelles encapsulating a quercetin-etoposide combination were developed to induce synergistic apoptotic effects and enhance direct drug delivery to the brain. However, the in vivo anticancer efficacy of the unmodified micelle formulation via intranasal administration remains limited. Therefore, this aims to investigate the enhancement of the formulation by conjugating the micelles with a novel and highly potent cell-penetrating peptide (CPP), RMMR1, identified using the intra-dermal delivery technology platform developed by REMEDI Co., Ltd. This modification seeks to enhance the brain-targeting capability of the micelles. The CPP-modified micelles encapsulating the quercetin-etoposide combination (CM(QE)) demonstrated superior in vivo brain-delivery efficiency and enhanced cellular uptake after intranasal administration. Furthermore, animal studies showed significant tumor reduction and increased survival rates, with no significant changes in body weight observed. These findings suggest that intranasal administration of CM(QE) holds promise as a significant advancement in chemotherapy for GBM.
多形性胶质母细胞瘤(GBM)是一种毁灭性的中枢神经系统原发性肿瘤,预后极差。治疗GBM的主要挑战在于血脑屏障(BBB)的限制性,阻碍了药物向大脑的有效递送。在本研究中,开发了包载槲皮素-依托泊苷组合的鼻内聚合物胶束,以诱导协同凋亡效应并增强药物向大脑的直接递送。然而,通过鼻内给药的未修饰胶束制剂的体内抗癌功效仍然有限。因此,本研究旨在通过将胶束与一种新型且高效的细胞穿透肽(CPP)RMMR1缀合来增强制剂效果,RMMR1是使用REMEDI有限公司开发的皮内递送技术平台鉴定出来的。这种修饰旨在增强胶束的脑靶向能力。包载槲皮素-依托泊苷组合的CPP修饰胶束(CM(QE))在鼻内给药后表现出优异的体内脑递送效率和增强的细胞摄取。此外,动物研究显示肿瘤显著缩小且存活率提高,同时未观察到体重有显著变化。这些发现表明,鼻内给药CM(QE)有望成为GBM化疗的一项重大进展。