Suppr超能文献

印度东北部一家三级医疗中心镰状细胞病患者的人口统计学、临床特征及治疗模式回顾性分析

A Retrospective Analysis of Demographics, Clinical Features, and Treatment Patterns in Sickle Cell Disease Patients at a Tertiary Healthcare Centre of North East India.

作者信息

Dutta Anupam, Dutta Taniya S, Shukla Amlin, Gogoi Papori

机构信息

General Medicine, Assam Medical College and Hospital, Dibrugarh, IND.

Pediatrics, Assam Medical College and Hospital, Dibrugarh, IND.

出版信息

Cureus. 2024 Nov 26;16(11):e74489. doi: 10.7759/cureus.74489. eCollection 2024 Nov.

Abstract

Background Sickle cell disease (SCD) is a hereditary disorder marked by abnormal hemoglobin (HbS), leading to chronic hemolytic anemia, vaso-occlusive crises (VOCs), and multi-organ complications. In India, the prevalence of SCD is highest among tribal populations in states like Madhya Pradesh, Maharashtra, Odisha, and Assam, with the disease burden exacerbated by limited healthcare access, especially in rural regions. This study provides a comprehensive analysis of the demographic profile, clinical features, and treatment patterns of SCD patients at a tertiary healthcare center in Upper Assam, where the prevalence of SCD is high among the tea tribe communities. Methods This retrospective observational study included 250 patients diagnosed with various SCD subtypes who presented with SCD-related complications at Assam Medical College and Hospital between January 2020 and December 2023. Data were obtained from medical records in the departments of medicine and pediatrics, covering demographic variables (age, gender, ethnicity), clinical characteristics (complications, hemoglobin levels, genotype, history of hospitalizations), and treatment details (frequency and type of blood transfusions, use of hydroxyurea and chelating agents). Descriptive statistics summarized demographic and clinical features, while chi-square tests and t-tests were used for bivariate analysis. Logistic regression identified factors associated with high transfusion requirements. Results The study population had a mean age of 17.2 years, with 54.4% male predominance. Most patients (87%) had sickle cell anemia (HbSS), while the remainder had other genotypes including HbSA, HbSE, and sickle cell thalassemia. The most common presenting symptoms were fever (61.2%) and bone/joint pain (48.4%), indicative of VOCs and frequent infections. Pallor (30%) and abdominal pain (25.6%) were also prominent. Half of the patients (125) received hydroxyurea, though its uptake was limited by availability and cost. A high transfusion burden was noted, with 72.4% of patients requiring between five to 12 transfusions annually. However, only 22.4% received chelation therapy to manage iron overload, reflecting the cost constraints in accessing these agents. Laboratory findings indicated a mean hemoglobin level of 7.19 g/dL and elevated serum ferritin levels due to repeated transfusions. The frequency of blood transfusions was higher compared to Western studies, emphasizing the need for more accessible disease-modifying therapies in resource-limited settings. Conclusions The findings of this study illustrate the significant clinical and transfusion burden experienced by SCD patients in Upper Assam. This population relies heavily on blood transfusions due to limited access to hydroxyurea and other advanced therapies. The study underscores a critical need for improved access to hydroxyurea, expanded availability of chelation therapy, and greater healthcare support for managing SCD-related complications in resource-limited settings. As India's National Sickle Cell Anemia Elimination Mission is implemented, regional studies such as this are essential for tailoring public health interventions to meet the specific needs of high-prevalence areas, especially among underserved tribal communities.

摘要

背景

镰状细胞病(SCD)是一种遗传性疾病,其特征为异常血红蛋白(HbS),可导致慢性溶血性贫血、血管闭塞性危机(VOCs)和多器官并发症。在印度,中央邦、马哈拉施特拉邦、奥里萨邦和阿萨姆邦等邦的部落人口中SCD患病率最高,医疗服务可及性有限,尤其是在农村地区,这加剧了疾病负担。本研究对阿萨姆邦上游一家三级医疗中心的SCD患者的人口统计学特征、临床特征和治疗模式进行了全面分析,该地区茶叶部落社区中SCD患病率很高。

方法

这项回顾性观察研究纳入了250例被诊断为各种SCD亚型且在2020年1月至2023年12月期间因SCD相关并发症到阿萨姆医学院和医院就诊的患者。数据来自内科和儿科的病历,涵盖人口统计学变量(年龄、性别、种族)、临床特征(并发症、血红蛋白水平、基因型、住院史)和治疗细节(输血频率和类型、羟基脲和螯合剂的使用情况)。描述性统计总结了人口统计学和临床特征,而卡方检验和t检验用于双变量分析。逻辑回归确定了与高输血需求相关的因素。

结果

研究人群的平均年龄为17.2岁,男性占比54.4%。大多数患者(87%)患有镰状细胞贫血(HbSS),其余患者具有其他基因型,包括HbSA、HbSE和镰状细胞地中海贫血。最常见的症状是发热(61.2%)和骨/关节疼痛(48.4%),提示存在VOCs和频繁感染。面色苍白(30%)和腹痛(25.6%)也很突出。一半的患者(125例)接受了羟基脲治疗,但其使用受到可用性和成本的限制。输血负担较重,72.4%的患者每年需要输血5至12次。然而,只有22.4%的患者接受螯合疗法来管理铁过载,这反映了获取这些药物的成本限制。实验室检查结果显示平均血红蛋白水平为7.19 g/dL,由于反复输血,血清铁蛋白水平升高。与西方研究相比,输血频率更高,这强调了在资源有限的环境中需要有更多可及的疾病改善疗法。

结论

本研究结果表明,阿萨姆邦上游的SCD患者承受着巨大的临床和输血负担。由于获取羟基脲和其他先进疗法的机会有限,这一人群严重依赖输血。该研究强调迫切需要改善羟基脲的可及性、扩大螯合疗法的可用性,并在资源有限的环境中为管理SCD相关并发症提供更多医疗支持。随着印度国家镰状细胞贫血消除任务的实施,这样的区域研究对于调整公共卫生干预措施以满足高患病率地区,特别是服务不足的部落社区的特定需求至关重要。

https://cdn.ncbi.nlm.nih.gov/pmc/blobs/d2b2/11670408/366cbfeec734/cureus-0016-00000074489-i01.jpg

文献AI研究员

20分钟写一篇综述,助力文献阅读效率提升50倍。

立即体验

用中文搜PubMed

大模型驱动的PubMed中文搜索引擎

马上搜索

文档翻译

学术文献翻译模型,支持多种主流文档格式。

立即体验