Suppr超能文献

极早期筛查淀粉样变性:游离轻链差异及IGLV基因使用作为λ单克隆丙种球蛋白病中轻链淀粉样变性的筛查变量

Seeking Amyloidosis Very Early: Free light Chain Differentials and IGLV Gene Use as Screening Variables for Light-chain Amyloidosis in λ Monoclonal Gammopathies.

作者信息

Zhou Ping, Mansukhani Mahesh M, Yeh Raymond, Lu Jiesheng, Xia Hongai, Koganti Lahari, Pang Jiuhong, Toskic Denis, Scalia Stephanie, Ma Xun, Lyons Nancy Coady, Fogaren Teresa, Varga Cindy, Comenzo Raymond L

机构信息

The John Conant Davis Myeloma and Amyloid Program, Tufts Medical Center, Boston, MA, USA.

Columbia University Laboratory of Personalized Genomic Medicine, Department of Pathology & Cell Biology, Columbia University Medical Center, New York, NY, USA.

出版信息

Br J Cancer Res. 2024 Jun;7(2):681-686. doi: 10.31488/bjcr.193. Epub 2024 May 23.

Abstract

BACKGROUND

Early diagnosis of systemic light-chain amyloidosis (AL) is needed because 25% of patients die within months of diagnosis. In patients with monoclonal gammopathy of undetermined significance (MGUS) or smoldering multiple myeloma (SMM) of the λ isotype, we explored the use of 2 screening variables: a free light chain difference of 23mg/L between λ and k and presence of IGLV genes that occur more frequently in AL.

METHODS

Patients contacted us and we sent HIPAA release and consent forms for discussion by phone. Their physicians were not involved. We enrolled patients with λ MGUS or SMM who met the FLC criteria with no prior biopsies showing amyloid. They sent us blood or marrow specimens for IGLV gene amplification by RT-PCR; we also assessed the feasibility of next generation sequencing (NGS) for IGLV genes. We informed patients and their physicians of results suggesting further evaluation for AL.

RESULTS

We enrolled 21 patients, 19 SMM and 2 MGUS, receiving blood (n=21) or marrow (n=5) specimens. We identified IGLV genes in 86% (18/21) of cases. Four of the 18 IGLV genes were not AL-related and 3 of these 4 progressed to myeloma requiring therapy; the 4th was screened for amyloid and was negative. Fourteen patients with AL-related genes had comprehensive evaluations and two with SMM had AL. RT-PCR and NGS identified the AL-related LV2-14 in those two and also the monoclonal IGLV genes from all of the marrow but not the peripheral blood samples.

CONCLUSION

We concluded that these variables may be useful in screening for AL in λ MGUS and SMM patients and acquired support for a small multi-center study employing marrow samples only.

摘要

背景

由于25%的系统性轻链淀粉样变性(AL)患者在确诊后的数月内死亡,因此需要对其进行早期诊断。在意义未明的单克隆丙种球蛋白病(MGUS)或λ亚型冒烟型多发性骨髓瘤(SMM)患者中,我们探索了两种筛查变量的应用:λ和κ之间游离轻链差值为23mg/L以及在AL中更频繁出现的IGLV基因的存在情况。

方法

患者与我们联系,我们发送了符合健康保险流通与责任法案(HIPAA)的信息披露和同意书,以便通过电话进行讨论。他们的医生未参与其中。我们纳入了符合游离轻链(FLC)标准且之前活检未显示淀粉样变的λ MGUS或SMM患者。他们将血液或骨髓样本寄给我们,用于通过逆转录聚合酶链反应(RT-PCR)进行IGLV基因扩增;我们还评估了下一代测序(NGS)用于IGLV基因检测的可行性。我们将提示对AL进行进一步评估的结果告知了患者及其医生。

结果

我们纳入了21例患者,其中19例为SMM,2例为MGUS,接收了血液样本(n = 21)或骨髓样本(n = 5)。我们在86%(18/21)的病例中鉴定出了IGLV基因。18个IGLV基因中有4个与AL无关,这4个中的3个进展为需要治疗的骨髓瘤;第4个接受了淀粉样变筛查,结果为阴性。14例具有与AL相关基因的患者接受了全面评估,其中2例SMM患者患有AL。RT-PCR和NGS在这两名患者中鉴定出了与AL相关的LV2-14基因,并且还从所有骨髓样本而非外周血样本中鉴定出了单克隆IGLV基因。

结论

我们得出结论,这些变量可能有助于筛查λ MGUS和SMM患者中的AL,并为仅采用骨髓样本的小型多中心研究获得了支持。

相似文献

本文引用的文献

5
Chromosome 1q21 abnormalities in multiple myeloma.多发性骨髓瘤中 1q21 染色体异常。
Blood Cancer J. 2021 Apr 29;11(4):83. doi: 10.1038/s41408-021-00474-8.

文献AI研究员

20分钟写一篇综述,助力文献阅读效率提升50倍。

立即体验

用中文搜PubMed

大模型驱动的PubMed中文搜索引擎

马上搜索

文档翻译

学术文献翻译模型,支持多种主流文档格式。

立即体验