Matsui Kenji, Watanabe Masahito, Yamamoto Shutaro, Kawagoe Shiho, Ikeda Takumi, Ohashi Hinari, Kuroda Takafumi, Koda Nagisa, Morimoto Keita, Kinoshita Yoshitaka, Inage Yuka, Saito Yatsumu, Fukunaga Shohei, Fujimoto Toshinari, Tajiri Susumu, Matsumoto Kei, Kobayashi Eiji, Yokoo Takashi, Yamanaka Shuichiro
Division of Nephrology and Hypertension, Department of Internal Medicine, The Jikei University School of Medicine, Tokyo, Japan.
Meiji University International Institute for Bio-Resource Research, Kanagawa, Japan.
Nat Commun. 2025 Mar 15;16(1):2572. doi: 10.1038/s41467-025-57795-6.
Fetal cell ablation models are crucial for studying congenital diseases, organ regeneration, and xenotransplantation. However, conventional knockout models offer limited control over disease severity, while conditional ablation models often require fetus-harming inducers. In the present study, we demonstrate that the inducible caspase 9 system enables precise targeting of fetal nephron progenitor cells in mice through the intrinsic apoptotic pathway. Using a safe, placenta-permeable inducer, this system facilitates specific, rapid, and efficient cell ablation. The system's temporal control allows precise adjustment of disease severity, generating reproducible models ranging from congenital kidney deficiency to severe chronic kidney disease. Cells with low expression levels of inducible caspase 9 and those in solid organs are less susceptible to apoptosis. However, this limitation can be overcome by inhibiting the X-linked inhibitor of apoptosis protein, thereby expanding the system's applicability. Additionally, this model provides a developmental environment suitable for chimeric kidney regeneration. This system advances understanding of induced cell death mechanisms, enhances pathological research tools, and supports therapeutic development in kidney disease and xenotransplantation applications.
胎儿细胞消融模型对于研究先天性疾病、器官再生和异种移植至关重要。然而,传统的基因敲除模型对疾病严重程度的控制有限,而条件性消融模型通常需要使用对胎儿有害的诱导剂。在本研究中,我们证明了可诱导的半胱天冬酶9系统能够通过内源性凋亡途径精确靶向小鼠胎儿肾祖细胞。使用一种安全的、可透过胎盘的诱导剂,该系统有助于特异性、快速且高效地进行细胞消融。该系统的时间控制允许精确调整疾病严重程度,生成从先天性肾发育不全到严重慢性肾病的可重复模型。可诱导的半胱天冬酶9表达水平低的细胞以及实体器官中的细胞对凋亡不太敏感。然而,通过抑制X连锁凋亡抑制蛋白可以克服这一局限性,从而扩大该系统的适用性。此外,该模型提供了适合嵌合肾再生的发育环境。该系统促进了对诱导性细胞死亡机制的理解,增强了病理研究工具,并支持了肾病和异种移植应用中的治疗开发。