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1
Correction: The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate.更正:PROPHECI试验:一项用于口服焦磷酸盐治疗弹性假黄瘤的II期、双盲、安慰剂对照、随机临床试验。
Trials. 2025 Apr 2;26(1):118. doi: 10.1186/s13063-025-08797-8.
2
The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate.PROPHECI试验:一项用于口服焦磷酸盐治疗弹性假黄瘤的II期双盲安慰剂对照随机临床试验。
Trials. 2025 Jan 29;26(1):30. doi: 10.1186/s13063-024-08666-w.
3
Lansoprazole Increases Inorganic Pyrophosphate in Patients with Pseudoxanthoma Elasticum: A Double-Blind, Randomized, Placebo-Controlled Crossover Trial.兰索拉唑增加弹性假黄瘤患者的无机焦磷酸:一项双盲、随机、安慰剂对照交叉试验。
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Etidronate for Prevention of Ectopic Mineralization in Patients With Pseudoxanthoma Elasticum.依替膦酸二钠预防弹性假黄瘤患者异位矿化。
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Oral supplementation of inorganic pyrophosphate in pseudoxanthoma elasticum.口服补充焦磷酸无机物治疗弹性假黄瘤。
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Choroidal neovascularization secondary to angioid streaks in a patient with pseudoxanthoma elasticum: case report.弹性假黄瘤患者中继发于血管样条纹的脉络膜新生血管形成:病例报告
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Functional Assessment of Missense Variants in the ABCC6 Gene Implicated in Pseudoxanthoma Elasticum, a Heritable Ectopic Mineralization Disorder.ABCC6 基因中错义变异与遗传性异位矿化疾病弹性假黄瘤的功能评估。
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Pseudoxanthoma Elasticum, Kidney Stones and Pyrophosphate: From a Rare Disease to Urolithiasis and Vascular Calcifications.弹性假黄瘤、肾结石和焦磷酸盐:从罕见疾病到尿石症和血管钙化。
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本文引用的文献

1
The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate.PROPHECI试验:一项用于口服焦磷酸盐治疗弹性假黄瘤的II期双盲安慰剂对照随机临床试验。
Trials. 2025 Jan 29;26(1):30. doi: 10.1186/s13063-024-08666-w.

Correction: The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate.

作者信息

Clotaire Laetitia, Rubera Isabelle, Duranton Christophe, Gal Jocelyn, Chamorey Emmanuel, Humeau Hélène, Yamani Samir, Chiaverini Christine, Willoteaux Serge, Padovani Bernard, Mourozeau Laurie, Mainguy Adam, Baillif Stéphanie, Martin Ludovic, Leftheriotis Georges

机构信息

Université Côte d'Azur, CNRS, LP2M, Nice, France.

Research and Development Department, Laboratoires ProNutri, Carros, France.

出版信息

Trials. 2025 Apr 2;26(1):118. doi: 10.1186/s13063-025-08797-8.

DOI:10.1186/s13063-025-08797-8
PMID:40176167
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC11966807/
Abstract
摘要