Schaller Eva, Lamer Stephanie, Schlosser Andreas, Stigloher Christian, Maher Pamela, Decker Michael
Julius-Maximilians-Universität Würzburg (JMU), Institute for Pharmacy and Food Chemistry, Pharmaceutical and Medicinal Chemistry, Am Hubland, 97074, Würzburg, Germany.
Julius-Maximilians-Universität Würzburg (JMU), Rudolf-Virchow-Zentrum - Center for Integrative and Translational Bioimaging, 97080, Würzburg, Germany.
Chemistry. 2025 Jun 12;31(33):e202501143. doi: 10.1002/chem.202501143. Epub 2025 May 19.
Phytocannabinoids are attracting growing attention because of their potential for treatment of neurodegenerative diseases. Among them, the "minor" cannabinoid, cannabinol (CBN), has emerged as a promising neuroprotective agent, acting independently of classical cannabinoid receptors through as-yet unidentified mitochondrial targets. To uncover the molecular basis of its neuroprotective effects, we designed and synthesized a chemical probe based on CBN, incorporating a minimalist diazirine linker. Functional assays confirmed that the probe retains CBN's mitochondrial activity and exhibits strong mitochondrial enrichment, as demonstrated by fluorescence microscopy and click-correlative light and electron microscopy (click-CLEM). By affinity-based protein profiling (AfBPP), we identified isocitrate dehydrogenase 2 (IDH2) as a key mitochondrial target of CBN. This finding was further substantiated by siRNA knockdown studies, which revealed that the absence of IDH2 partially phenocopies CBN's effects, validating its role as a critical mediator of CBN's neuroprotective activity.
植物大麻素因其在治疗神经退行性疾病方面的潜力而受到越来越多的关注。其中,“次要”大麻素大麻酚(CBN)已成为一种有前景的神经保护剂,它通过尚未明确的线粒体靶点独立于经典大麻素受体发挥作用。为了揭示其神经保护作用的分子基础,我们设计并合成了一种基于CBN的化学探针,其中包含一个简约的重氮丙啶连接子。功能测定证实,该探针保留了CBN的线粒体活性,并表现出强烈的线粒体富集,荧光显微镜以及点击相关光电子显微镜(click-CLEM)均证明了这一点。通过基于亲和力的蛋白质谱分析(AfBPP),我们确定异柠檬酸脱氢酶2(IDH2)是CBN的关键线粒体靶点。siRNA敲低研究进一步证实了这一发现,该研究表明IDH2的缺失部分模拟了CBN的作用,验证了其作为CBN神经保护活性关键介质的作用。