Brown Harry J, Fan Rebecca Z, Bell Riley, Salehe Said S, Martínez Carlos Martínez, Lai Yanhao, Tieu Kim
College of Arts and Sciences, Florida International University, Miami, FL, United States of America; Department of Environmental Health Sciences, Florida International University, Miami, FL, United States of America; Biomolecular Sciences Institute, Florida International University, Miami, FL, United States of America.
Department of Environmental Health Sciences, Florida International University, Miami, FL, United States of America.
Neurobiol Dis. 2025 Aug;212:106976. doi: 10.1016/j.nbd.2025.106976. Epub 2025 May 26.
Emerging studies have shown that dysregulation in mitochondrial dynamics has a major negative impact on mitochondria. Partial genetic and pharmacological inhibition of the mitochondrial fission dynamin-related protein 1 (DRP1) has been demonstrated to be beneficial in models of neurodegenerative disorders, including Parkinson's disease (PD). However, the expression of DRP1 and other mitochondrial fission/fusion mediators have not been investigated in the brains of Parkinson's patients. This information is critical to strengthening mitochondrial dynamics as a potential therapeutic target for PD. We report in this study that significant increases in the levels of both DNM1L, which encodes DRP1, as well as the DRP1 protein were detected in Parkinson's patients. Immunostaining revealed increased DRP1 expression in dopamine (DA) neurons, astrocytes, and microglia. In addition to DRP1, the levels of other fission and fusion genes/proteins were also altered. To complement these human studies and given the significant role of α-synuclein in PD pathogenesis, we performed time-course studies using transgenic mice overexpressing human wild-type SNCA. As early as six months old, we detected an upregulation of DRP1 in the nigral DA neurons of the SNCA mice as compared to their wild-type littermates. Furthermore, these mutant animals exhibited more DRP1 phosphorylation at serine 616, which promotes its translocation to mitochondria to induce fragmentation. Together, this study shows an upregulation of DRP1 and alterations in other fission/fusion proteins in both human and mouse PD brains, leading to a pro-fission phenotype, providing additional evidence that blocking mitochondrial fission or promoting fusion is a potential therapeutic strategy for PD.
新兴研究表明,线粒体动力学失调对线粒体有重大负面影响。线粒体分裂动力相关蛋白1(DRP1)的部分基因和药理学抑制已被证明在包括帕金森病(PD)在内的神经退行性疾病模型中是有益的。然而,尚未在帕金森病患者的大脑中研究DRP1和其他线粒体分裂/融合介质的表达。这些信息对于强化线粒体动力学作为PD的潜在治疗靶点至关重要。我们在本研究中报告,在帕金森病患者中检测到编码DRP1的DNM1L水平以及DRP1蛋白水平均显著增加。免疫染色显示多巴胺(DA)神经元、星形胶质细胞和小胶质细胞中DRP1表达增加。除了DRP1,其他分裂和融合基因/蛋白的水平也发生了改变。为了补充这些人体研究,并鉴于α-突触核蛋白在PD发病机制中的重要作用,我们使用过表达人野生型SNCA的转基因小鼠进行了时间进程研究。早在六个月大时,我们就检测到与野生型同窝小鼠相比,SNCA小鼠黑质DA神经元中DRP1上调。此外,这些突变动物在丝氨酸616处表现出更多的DRP1磷酸化,这促进了其向线粒体的转位以诱导碎片化。总之,本研究表明在人和小鼠的PD大脑中DRP1上调以及其他分裂/融合蛋白发生改变,导致促分裂表型,为阻断线粒体分裂或促进融合是PD的潜在治疗策略提供了额外证据。