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China's first approved gene therapy for hemophilia B: A new era for global AAV-based treatments.

作者信息

Wei Hongying, Xiao Weidong, Dai Jing

机构信息

Department of Pediatrics, The Second Affiliated Hospital of Guangxi Medical University, Nanning, Guangxi, P.R. China.

Department of Pediatrics, Herman B Wells Center for Pediatric Research, Indiana University School of Medicine, Indianapolis, IN 46202, USA.

出版信息

Mol Ther. 2025 Jun 4;33(6):2312-2313. doi: 10.1016/j.ymthe.2025.05.014. Epub 2025 May 28.

DOI:10.1016/j.ymthe.2025.05.014
PMID:40441148
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC12172263/
Abstract
摘要

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引用本文的文献

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Recent Advances in Gene Therapy for Hemophilia.血友病基因治疗的最新进展
Clin Appl Thromb Hemost. 2025 Jan-Dec;31:10760296251378455. doi: 10.1177/10760296251378455. Epub 2025 Sep 10.