de Almeida Monique Marylin Alves, Kornfeld Samantha F, De Repentigny Yves, Al-Aarg Majd, Ghani Ibrahim, Cummings Sarah E, Sutton Emma R, Yaworski Rebecca, McKay Kelsea S, Gagnon Sabrina, Beauvais Ariane, Kothary Rashmi
Regenerative Medicine Program, Ottawa Hospital Research Institute, Ottawa K1H 8L6, Canada; Centre for Neuromuscular Disease, University of Ottawa, K1H 8M5, Canada.
Regenerative Medicine Program, Ottawa Hospital Research Institute, Ottawa K1H 8L6, Canada; Department of Cellular and Molecular Medicine, University of Ottawa, Ottawa K1H 8M5, Canada.
Neurobiol Dis. 2025 Sep;213:106999. doi: 10.1016/j.nbd.2025.106999. Epub 2025 Jun 10.
Multiple sclerosis (MS) is a progressive inflammatory disease of the central nervous system (CNS) marked by myelin loss, which impairs nerve function. Current therapies fail to halt disease progression or prevent myelin and axonal degeneration. In this study, we explored the impact of miR-145 loss in a murine model of experimental autoimmune encephalomyelitis (EAE), which mimics MS pathology. Loss of miR-145 reduced clinical severity and significantly decreased immune cell infiltration in the lumbar spinal cord during both the onset and chronic stages of the disease. Additionally, miR-145 loss altered the expression of key inflammatory genes and modulated astrocytic activity throughout EAE. Of significant interest, acute treatment with an antisense oligonucleotide (ASO) targeting miR-145 decreased miR-145 levels and led to reduced disease severity, decreased immune cell infiltration, and an increase in regulatory T cells in EAE mice. Moreover, miR-145 deficiency mitigated axon and myelin degeneration. Our findings suggest that ASOs targeting miR-145 may offer a promising therapeutic strategy, addressing both inflammatory and degenerative components of MS.
多发性硬化症(MS)是一种中枢神经系统(CNS)的进行性炎症性疾病,其特征是髓鞘丢失,这会损害神经功能。目前的治疗方法无法阻止疾病进展或预防髓鞘和轴突变性。在本研究中,我们在实验性自身免疫性脑脊髓炎(EAE)小鼠模型中探究了miR-145缺失的影响,该模型模拟了MS病理。miR-145的缺失降低了临床严重程度,并在疾病的发作期和慢性期均显著减少了腰脊髓中的免疫细胞浸润。此外,miR-145的缺失改变了关键炎症基因的表达,并在整个EAE过程中调节了星形胶质细胞的活性。值得关注的是,用靶向miR-145的反义寡核苷酸(ASO)进行急性治疗可降低miR-145水平,并导致EAE小鼠的疾病严重程度降低、免疫细胞浸润减少以及调节性T细胞增加。此外,miR-145缺乏减轻了轴突和髓鞘变性。我们的研究结果表明,靶向miR-145的ASO可能提供一种有前景的治疗策略,可解决MS的炎症和变性成分。