Elgehiny Amr, Hsu Alexander, McCall David, Gibson Amber, Cuglievan Branko, Nunez Cesar, Garcia Miriam B, Castellanos Luz, Funck Alexander, Razvi Shehla
Department of Pediatrics.
Division of Internal Medicine, Department of Endocrine Neoplasia and Hormonal Disorders, The University of Texas MD Anderson Cancer Center, Houston, TX.
J Pediatr Hematol Oncol. 2025 Aug 1;47(6):e215-e221. doi: 10.1097/MPH.0000000000003077. Epub 2025 Jun 25.
Pegylated asparaginase is now standard in US treatment protocols for acute lymphoblastic leukemia (ALL). However, they are associated with significant side effects, including severe hypertriglyceridemia. In this case series, we report 8 patients with severe (triglyceride >1000 mg/dL) hypertriglyceridemia after receiving long-acting asparaginase for ALL and describe their clinical course. The 8 patients included 3 females and 5 males (aged 2 to 14 y; median=12 y); 7 were Hispanic and 1 was Middle Eastern. The median time from dose to peak hypertriglyceridemia was 17 days and to resolution was 25 days. Presentations included isolated hypertriglyceridemia, pseudohyponatremia, hypoglycemia, and lipemia interfering with complete blood count results. Median length of hospitalization was 3.5 days. Management included hydration, a low-fat diet, omega-3 supplements, fenofibrates, statins, and levocarnitine. An insulin drip was used in 2 patients in the intensive care unit. Asparaginase treatment continued per protocol after triglyceride levels were <1000 mg/dL. In conclusion, severe hypertriglyceridemia can occur after long-acting asparaginase and is typically asymptomatic and transient, not requiring a pause or modification in treatment. We recommend monitoring for hypertriglyceridemia closely in patients with risk factors who are resuming long-acting asparaginase therapy after triglyceride levels fall <1000 mg/dL.
聚乙二醇化天冬酰胺酶目前在美国急性淋巴细胞白血病(ALL)的治疗方案中是标准用药。然而,它们会引发显著的副作用,包括严重的高甘油三酯血症。在这个病例系列中,我们报告了8例在接受长效天冬酰胺酶治疗ALL后出现严重(甘油三酯>1000mg/dL)高甘油三酯血症的患者,并描述了他们的临床病程。这8例患者包括3名女性和5名男性(年龄2至14岁;中位数=12岁);7名是西班牙裔,1名是中东人。从用药到甘油三酯血症峰值的中位时间为17天,恢复正常的中位时间为25天。临床表现包括单纯性高甘油三酯血症、假性低钠血症、低血糖以及脂血症干扰全血细胞计数结果。住院时间中位数为3.5天。治疗措施包括补液、低脂饮食、ω-3补充剂、非诺贝特、他汀类药物和左卡尼汀。重症监护病房的2例患者使用了胰岛素静脉滴注。甘油三酯水平<1000mg/dL后,按照方案继续使用天冬酰胺酶治疗。总之,长效天冬酰胺酶治疗后可能会出现严重的高甘油三酯血症,通常无症状且为短暂性,不需要暂停或调整治疗。我们建议对有风险因素且在甘油三酯水平降至<1000mg/dL后恢复长效天冬酰胺酶治疗的患者密切监测高甘油三酯血症。