Wang Xiaoyang, Xia Yingjie, Guo Maggie Suisui, Wu Jiahui, Dilidaer Ajiaikebaier, Gao Jin, Dong Tina Tingxia, Zhu Yue, Tsim Karl Wah Keung
Division of Life Science, Center for Chinese Medicine and State Key Laboratory of Molecular Neuroscience, The Hong Kong University of Science and Technology, Hong Kong, China.
Shenzhen Key Laboratory of Edible and Medicinal Bioresources, The Hong Kong University of Science and Technology, Shenzhen, China.
J Neurochem. 2025 Aug;169(8):e70178. doi: 10.1111/jnc.70178.
Alzheimer's disease (AD) is the most common dementia with progressive loss of cognitive functions. Acetylcholinesterase (AChE) inhibitors have been approved as conventional pharmacotherapies for AD. Tacrine was the first AChE inhibitor introduced into clinics for AD; however, it was withdrawn from use in 2013 because of safety concerns. In cultured neurons, as well as in mice, tacrine was found to induce endoplasmic reticulum (ER) stress and finally lead to cell apoptosis: the event was triggered by binding the inhibitor to the intracellular enzyme serving as a pharmacological chaperone. Trehalose, a known ER stress reducer, was shown here to ameliorate the ER stress induced by tacrine in AChE-overexpressed NG108-15 cells, with the increased level of C/EBP homologous protein (CHOP) and phosphorylated eukaryotic initiation factor 2 alpha (p-eIF2α). In tetrameric G4 AChE overexpressed cells, the tacrine-exposed cultures revealed considerable G1/G2 forms of AChE accumulated in the ER fraction, whereas the treatment of trehalose decreased the accumulation of G1/G2 AChE. Meanwhile, trehalose reduced the ER stress induced by other AChE inhibitors, for example, lycobetaine, bis(3)-cognitin, daurisoline, and dauricine, in the cultured neuronal cells. Besides, this tacrine-induced ER stress was identified in all AChE isoforms, as well as in butyrylcholinesterase (BChE) expressing cells. Thus, we proposed that the AChE inhibitors, particularly tacrine, could act as 'chemical/pharmacological chaperones' during AChE biosynthesis in the ER, disrupting the proper folding of AChE in neurons as a result of ER stress. Trehalose possesses the ability to relieve ER stress by promoting the proper assembly of AChE. The results provide guidance for the drug design and discovery of AChE inhibitors for AD treatment.
阿尔茨海默病(AD)是最常见的痴呆症,伴有认知功能的进行性丧失。乙酰胆碱酯酶(AChE)抑制剂已被批准作为AD的传统药物疗法。他克林是第一种引入临床用于治疗AD的AChE抑制剂;然而,由于安全问题,它于2013年被停用。在培养的神经元以及小鼠中,发现他克林会诱导内质网(ER)应激并最终导致细胞凋亡:该事件是由抑制剂与作为药理学伴侣的细胞内酶结合引发的。海藻糖是一种已知的ER应激减轻剂,在此处显示可改善他克林在过表达AChE的NG108 - 15细胞中诱导的ER应激,同时C/EBP同源蛋白(CHOP)水平和磷酸化真核起始因子2α(p - eIF2α)升高。在过表达四聚体G4 AChE的细胞中,暴露于他克林的培养物显示在内质网部分积累了大量G1/G2形式的AChE,而海藻糖处理减少了G1/G2 AChE的积累。同时,海藻糖降低了其他AChE抑制剂(例如石蒜碱、双(3)- 认知素、蝙蝠葛碱和蝙蝠葛苏林碱)在培养的神经元细胞中诱导的ER应激。此外,这种他克林诱导的ER应激在所有AChE同工型以及表达丁酰胆碱酯酶(BChE)的细胞中均被发现。因此,我们提出AChE抑制剂,特别是他克林,在ER中AChE生物合成过程中可作为“化学/药理学伴侣”,由于ER应激导致神经元中AChE的正确折叠受到破坏。海藻糖具有通过促进AChE的正确组装来减轻ER应激的能力。这些结果为AD治疗的AChE抑制剂的药物设计和发现提供了指导。