Li Leyi, Ray Arnab, Xue Shifeng
Department of Biological Sciences, National University of Singapore, Singapore.
Department of Biological Sciences, National University of Singapore, Singapore.
Curr Opin Cell Biol. 2025 Oct;96:102579. doi: 10.1016/j.ceb.2025.102579. Epub 2025 Aug 19.
DUX4 is a transcription factor with a critical role in zygotic genome activation. It is expressed briefly in early embryogenesis and shut off for the rest of life. Inappropriate reactivation of DUX4 in adult muscle cells causes facioscapulohumeral dystrophy (FSHD), a muscular dystrophy affecting up to 1 in 8000, currently with no cure. In healthy adults, DUX4 is kept repressed through a variety of epigenetic mechanisms. Here, we explore the regulation of DUX4 in both embryogenesis and adulthood to identify similarities and differences. Comparative insights into DUX4 regulation can also be gained by studying its mouse homologue, Dux, which plays a similar role in early embryogenesis. Despite being in different genomic environments, Dux and DUX4 share similar regulatory mechanisms. We propose that the mechanisms regulating Dux and DUX4 in embryogenesis could inspire novel therapeutic angles for FSHD.
DUX4是一种转录因子,在合子基因组激活中起关键作用。它在胚胎发育早期短暂表达,之后在余生中关闭。成人肌肉细胞中DUX4的不适当重新激活会导致面肩肱型肌营养不良症(FSHD),这是一种影响高达八千分之一人群的肌肉萎缩症,目前尚无治愈方法。在健康成年人中,DUX4通过多种表观遗传机制保持抑制状态。在这里,我们探讨了胚胎发育和成年期DUX4的调控,以确定异同。通过研究其小鼠同源物Dux,也可以获得对DUX4调控的比较性见解,Dux在早期胚胎发育中起类似作用。尽管处于不同的基因组环境中,Dux和DUX4共享相似的调控机制。我们提出,在胚胎发育中调节Dux和DUX4的机制可能为FSHD带来新的治疗思路。