van de Donk Niels W C J, Bahlis Nizar J, Pawlyn Charlotte, Gay Francesca, Mateos Maria-Victoria, Weisel Katja, Lonial Sagar, Richardson Paul G
Department of Hematology, Cancer Center Amsterdam, Amsterdam University Medical Center, Vrije Universiteit Amsterdam, Amsterdam, Netherlands.
Arnie Charbonneau Cancer Institute, University of Calgary, Calgary, AB, Canada.
Onco Targets Ther. 2025 Aug 27;18:921-933. doi: 10.2147/OTT.S398118. eCollection 2025.
Although recent decades have seen continued improvements in survival for patients with multiple myeloma, the disease remains largely incurable, and most patients will experience relapse and/or become refractory to treatment. There thus remains an urgent unmet need for novel treatments, particularly for those patients with relapsed or refractory multiple myeloma. Novel treatment modalities, such as targeted protein degradation, have attracted particular interest due to their ability to expand the range of druggable protein targets in myeloma cells. Iberdomide (CC-220) and mezigdomide (CC-92480) are promising oral CELMoD™ agents currently being evaluated for the treatment of patients with multiple myeloma. Preclinical data from lenalidomide- and pomalidomide-resistant cell lines and mouse models suggest that iberdomide and mezigdomide have the potential to provide therapeutic benefit even in patients who are refractory to lenalidomide and pomalidomide. The optimized specificity, potency, and safety profile of iberdomide and mezigdomide supports their clinical use and aligns with the need for longer durations of a well-tolerated oral CELMoD agent with synergistic combinability with other immune approaches (such as anti-CD38 monoclonal antibodies) and proteasome inhibitors (such as bortezomib and carfilzomib). Although neither iberdomide or mezigdomide has yet received regulatory approval for the treatment of multiple myeloma, based on their mechanism of action and the data available to date, we propose that both drugs may be attractive options for the treatment of patients with relapsed or refractory multiple myeloma; based on their efficacy and safety profiles, iberdomide is likely better suited for use in newly diagnosed, first relapse, or maintenance settings, whereas mezigdomide may also be better suited for use in patients with early relapse or a greater number of prior antimyeloma treatments. Iberdomide and mezigdomide are currently being evaluated for the treatment of patients with multiple myeloma in several trials, and results so far are promising.
尽管近几十年来多发性骨髓瘤患者的生存率持续提高,但该疾病在很大程度上仍无法治愈,大多数患者会经历复发和/或对治疗产生耐药。因此,对于新型治疗方法仍有迫切未满足的需求,特别是对于那些复发或难治性多发性骨髓瘤患者。新型治疗方式,如靶向蛋白降解,因其能够扩大骨髓瘤细胞中可成药蛋白靶点的范围而备受关注。伊布多米德(CC-220)和美齐多米德(CC-92480)是有前景的口服CELMoD™药物,目前正在评估用于治疗多发性骨髓瘤患者。来自来那度胺和泊马度胺耐药细胞系及小鼠模型的临床前数据表明,即使在对来那度胺和泊马度胺耐药的患者中,伊布多米德和美齐多米德也有可能提供治疗益处。伊布多米德和美齐多米德优化的特异性、效力和安全性特征支持它们的临床应用,并且符合对具有良好耐受性的口服CELMoD药物的需求,该药物具有与其他免疫方法(如抗CD38单克隆抗体)和蛋白酶体抑制剂(如硼替佐米和卡非佐米)协同联合的能力。尽管伊布多米德或美齐多米德尚未获得治疗多发性骨髓瘤的监管批准,但基于它们的作用机制和现有数据,我们认为这两种药物可能是治疗复发或难治性多发性骨髓瘤患者的有吸引力的选择;基于它们的疗效和安全性特征,伊布多米德可能更适合用于新诊断、首次复发或维持治疗,而美齐多米德可能也更适合用于早期复发或接受过更多先前抗骨髓瘤治疗的患者。目前正在多项试验中评估伊布多米德和美齐多米德治疗多发性骨髓瘤患者的效果,到目前为止结果很有前景。