Guttman-Yassky Emma, Simpson Eric, Esfandiari Ehsanollah, Mano Hirotaka, Bauer Jillian, Charuworn Prista, Kabashima Kenji
Department of Dermatology and Department of Allergy and Immunology, Icahn School of Medicine at Mount Sinai, New York, NY, 10029-6574, USA.
Department of Dermatology, Oregon Health & Science University, Portland, OR, USA.
Dermatol Ther (Heidelb). 2025 Sep 6. doi: 10.1007/s13555-025-01492-1.
Atopic dermatitis (AD) is a chronic inflammatory disease characterized by eczematous skin lesions, intense pruritus, skin pain, sleep disruption, and mental health disturbances. There remains a need for a therapeutic option that delivers durable efficacy, safety, and convenient dosing across the AD patient population. This review provides an overview of AD pathogenesis driven by T-cell imbalance and describes a novel therapeutic option targeting the OX40 receptor, a costimulatory molecule expressed specifically on activated T cells. Expression of the OX40 receptor on skin-homing T cells is increased in AD. OX40-mediated activation of pathogenic T cells drives inflammation in AD and is critical for the formation of memory T cells, leading to persistent disease. Rocatinlimab (AMG 451/KHK4083) is a novel T-cell rebalancing therapy that inhibits and reduces pathogenic T cells by targeting the OX40 receptor. By reducing pathogenic T-cell number and activity, rocatinlimab has the potential to limit AD flares and modify the course of disease. Rocatinlimab showed promise for the treatment of moderate-to-severe AD in a phase 2b trial, significantly improving overall disease severity, skin involvement, pruritus, sleep disturbance, and quality of life compared with placebo at week 16. Improvements continued through week 36 during active treatment, and notably, were largely maintained in responders throughout a subsequent 20-week off-treatment period, providing evidence for durable on and off treatment responses. Rocatinlimab has also demonstrated a favorable safety and tolerability profile. A large, global phase 3 program (ROCKET) including eight studies is underway to further assess the efficacy, safety, maintenance of response, extended dosing, and off-treatment durability of rocatinlimab in adults and adolescents with moderate-to-severe AD.
特应性皮炎(AD)是一种慢性炎症性疾病,其特征为湿疹样皮肤病变、剧烈瘙痒、皮肤疼痛、睡眠障碍和心理健康问题。仍然需要一种能在AD患者群体中提供持久疗效、安全性和便捷给药方式的治疗选择。本综述概述了由T细胞失衡驱动的AD发病机制,并描述了一种针对OX40受体的新型治疗选择,OX40受体是一种在活化T细胞上特异性表达的共刺激分子。AD患者皮肤归巢T细胞上OX40受体的表达增加。OX40介导的致病性T细胞活化驱动AD炎症,对记忆T细胞的形成至关重要,导致疾病持续存在。罗卡替尼单抗(AMG 451/KHK4083)是一种新型T细胞再平衡疗法,通过靶向OX40受体抑制并减少致病性T细胞。通过减少致病性T细胞数量和活性,罗卡替尼单抗有可能限制AD发作并改变疾病进程。在一项2b期试验中,罗卡替尼单抗显示出治疗中度至重度AD的前景,与安慰剂相比,在第16周时显著改善了整体疾病严重程度、皮肤受累情况、瘙痒、睡眠障碍和生活质量。在积极治疗期间,改善持续到第36周,值得注意的是,在随后20周的停药期,反应者的改善情况在很大程度上得以维持,为治疗期间和停药后的持久反应提供了证据。罗卡替尼单抗还表现出良好的安全性和耐受性。一项包括八项研究的大型全球3期项目(ROCKET)正在进行中,以进一步评估罗卡替尼单抗在中度至重度AD成人和青少年中的疗效、安全性、反应维持情况、延长给药和停药后耐久性。