Shahzad Moazzam, Amin Muhammad Kashif, Badar Talha
Division of Hematology and Oncology, Moffitt Cancer Center, Tampa, FL 33612, USA.
Division of Hematologic Malignancies & Cellular Therapeutics, The University of Kansas Medical Center, Kansas City, KS 66103, USA.
Cancers (Basel). 2025 Aug 23;17(17):2746. doi: 10.3390/cancers17172746.
The therapeutic landscape of adults with B-cell precursor acute lymphoblastic leukemia (BCP-ALL) is undergoing a paradigm shift, driven by the development of immunotherapy-based "chemo-free" and "chemo-light' regimens. These strategies aim to achieve high efficacy with reduced toxicity, particularly in older adults who may not tolerate intensive chemotherapy. In Philadelphia chromosome-positive (Ph+) BCP-ALL, the incorporation of ABL tyrosine kinase inhibitors (TKIs) with blinatumomab (CD3/CD19 bispecific T-cell engager) has shown remarkable efficacy, with some studies reporting molecular response rates in the range of 90-100% and long-term survival exceeding 80% without the need for intensive chemotherapy or allogeneic hematopoietic cell transplantation (allo-HCT). In Philadelphia-negative (Ph-) BCP- ALL, an immunotherapy-based combination of blinatumomab and inotuzumab ozogamicin (anti-CD22 antibody-drug conjugate) has demonstrated high rates of complete remission and measurable residual disease (MRD) negativity, with manageable toxicity. While chimeric antigen receptor (CAR) T-cell therapy remains a transformative option for relapsed/refractory B-ALL, its integration into frontline treatment is still under investigation. Ongoing trials are evaluating the optimal sequencing and combinations of these agents and their potential to obviate the need for chemotherapy and/or allo-HCT in selected patients. As evidence continues to accumulate, chemo-free and chemo-light regimens, incorporating minimal chemotherapy with targeted agents to balance efficacy and reduced toxicity, are poised to redefine the standard of care for adults BCP-ALL, offering the possibility of durable remissions with reduced treatment-related morbidity.
在基于免疫疗法的“无化疗”和“轻化疗”方案的推动下,B细胞前体急性淋巴细胞白血病(BCP-ALL)成人患者的治疗格局正在发生范式转变。这些策略旨在在降低毒性的同时实现高效,特别是对于可能无法耐受强化化疗的老年患者。在费城染色体阳性(Ph+)BCP-ALL中,将ABL酪氨酸激酶抑制剂(TKIs)与博纳吐单抗(CD3/CD19双特异性T细胞衔接器)联合使用已显示出显著疗效,一些研究报告分子缓解率在90%-100%范围内,长期生存率超过80%,无需强化化疗或异基因造血细胞移植(allo-HCT)。在费城染色体阴性(Ph-)BCP-ALL中,基于免疫疗法的博纳吐单抗和奥英妥珠单抗(抗CD22抗体-药物偶联物)联合使用已证明完全缓解率和可测量残留病(MRD)阴性率很高,且毒性可控。虽然嵌合抗原受体(CAR)T细胞疗法仍然是复发/难治性B-ALL的一种变革性选择,但其纳入一线治疗仍在研究中。正在进行试验评估这些药物的最佳序贯和联合使用方式,以及它们在特定患者中避免化疗和/或allo-HCT的潜力。随着证据不断积累,将最小化化疗与靶向药物相结合以平衡疗效和降低毒性的无化疗和轻化疗方案,有望重新定义成人BCP-ALL的护理标准,提供实现持久缓解并降低治疗相关发病率的可能性。