Matarneh Ahmad, Matarneh Bayan, Salameh Omar, Akkari Abdelrauof, Ghahramani Nasrollah, Trivedi Naman
Department of Nephrology, Penn State Milton S. Hershey Medical Center, Hershey, PA, USA.
Detroit Medical Center, Children's Hospital, Detroit, MI, USA.
Clin Rev Allergy Immunol. 2025 Nov 27;68(1):103. doi: 10.1007/s12016-025-09114-6.
Systemic lupus erythematosus (SLE) is a chronic, multisystem autoimmune disorder characterized by loss of self-tolerance, immune complex deposition, and progressive organ damage. Despite advances in immunosuppressive therapy, a subset of patients develops treatment-resistant or refractory manifestations; terms used variably in the literature to describe inadequate response to multiple standard immunosuppressants. Chimeric antigen receptor T cell (CAR-T) therapy, a revolutionary modality in oncology, is now emerging as a promising approach in severe autoimmune diseases including SLE. By redirecting autologous T cells to target B cell antigens such as CD19 or BCMA, CAR-T therapy enables deep and sustained B cell depletion, potentially resetting immune tolerance.Early case series have reported encouraging remission rates and serologic improvements in refractory SLE; however, these observations derive from small, uncontrolled studies. The long-term durability, relapse risk, safety profile, and cost-effectiveness of CAR-T therapy in autoimmune disease remain uncertain and require confirmation in larger, controlled trials. This narrative review synthesizes the current understanding of CAR-T therapy in SLE, covering immunopathogenesis, rationale for B cell targeting, CAR-T mechanisms, preclinical evidence, clinical outcomes, safety considerations, and future directions. We integrate data from peer-reviewed studies, conference abstracts, and preprints up to August 2025, and propose a framework for integrating CAR-T into the treatment paradigm for refractory SLE.
系统性红斑狼疮(SLE)是一种慢性多系统自身免疫性疾病,其特征为自身耐受性丧失、免疫复合物沉积和进行性器官损害。尽管免疫抑制治疗取得了进展,但仍有一部分患者出现对治疗耐药或难治的表现;文献中使用的术语各不相同,用于描述对多种标准免疫抑制剂反应不足的情况。嵌合抗原受体T细胞(CAR-T)疗法是肿瘤学中的一种革命性治疗方式,目前正成为包括SLE在内的严重自身免疫性疾病的一种有前景的治疗方法。通过将自体T细胞重定向以靶向B细胞抗原如CD19或BCMA,CAR-T疗法能够实现深度且持续的B细胞清除,有可能重置免疫耐受性。早期病例系列报道了难治性SLE令人鼓舞的缓解率和血清学改善情况;然而,这些观察结果来自小型、非对照研究。CAR-T疗法在自身免疫性疾病中的长期疗效、复发风险、安全性和成本效益仍不确定,需要在更大规模的对照试验中得到证实。这篇叙述性综述综合了目前对SLE中CAR-T疗法的认识,涵盖免疫发病机制、靶向B细胞的原理、CAR-T机制、临床前证据、临床结果、安全考虑因素和未来方向。我们整合了截至2025年8月来自同行评审研究、会议摘要和预印本的数据,并提出了一个将CAR-T纳入难治性SLE治疗模式的框架。