Gene therapy for cystic fibrosis using cationic liposome mediated gene transfer: a phase I trial of safety and efficacy in the nasal airway.

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作者信息

Sorscher E J, Logan J J, Frizzell R A, Lyrene R K, Bebok Z, Dong J Y, Duvall M D, Felgner P L, Matalon S, Walker L

出版信息

Hum Gene Ther. 1994 Oct;5(10):1259-77. doi: 10.1089/hum.1994.5.10-1259.

DOI:10.1089/hum.1994.5.10-1259

PMID:7531503

Abstract

摘要

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Gene therapy for cystic fibrosis using cationic liposome mediated gene transfer: a phase I trial of safety and efficacy in the nasal airway.

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