Biochemical and immunological status following gene therapy and PEG-ADA therapy for adenosine deaminase (ADA) deficiency.
作者信息
Fairbanks L D, Simmonds H A, Hoogerbrugge P M, van Beusechem V W, Valerio D, Moseley A, Levinsky R J, Gaspar H B, Morgan G
机构信息
Molecular Immunology Unit, UMDS Guy's Hospital, London, GB.
出版信息
Adv Exp Med Biol. 1994;370:391-4. doi: 10.1007/978-1-4615-2584-4_85.
PMID:7660936
Abstract
摘要
相似文献
1
Biochemical and immunological status following gene therapy and PEG-ADA therapy for adenosine deaminase (ADA) deficiency.基因治疗和聚乙二醇化腺苷脱氨酶（PEG-ADA）治疗腺苷脱氨酶（ADA）缺乏症后的生化和免疫状态。
Adv Exp Med Biol. 1994;370:391-4. doi: 10.1007/978-1-4615-2584-4_85.
2
Enzyme replacement therapy with polyethylene glycol-adenosine deaminase in adenosine deaminase deficiency: overview and case reports of three patients, including two now receiving gene therapy.聚乙二醇化腺苷脱氨酶用于腺苷脱氨酶缺乏症的酶替代疗法：概述及三例患者病例报告，其中两例患者目前正在接受基因治疗。
Pediatr Res. 1993 Jan;33(1 Suppl):S42-7; discussion S47-8. doi: 10.1203/00006450-199305001-00236.
3
Genetic manipulation of hematopoietic stem cells in adenosine deaminase deficiency.
Adv Exp Med Biol. 1994;370:395-400. doi: 10.1007/978-1-4615-2584-4_86.
4
PEG-ADA: an alternative to haploidentical bone marrow transplantation and an adjunct to gene therapy for adenosine deaminase deficiency.聚乙二醇化腺苷脱氨酶：单倍体相合骨髓移植的替代方法及腺苷脱氨酶缺乏症基因治疗的辅助手段
Hum Mutat. 1995;5(2):107-12. doi: 10.1002/humu.1380050202.
5
Long-term efficacy of enzyme replacement therapy for adenosine deaminase (ADA)-deficient severe combined immunodeficiency (SCID).腺苷脱氨酶（ADA）缺乏的重症联合免疫缺陷（SCID）的酶替代疗法的长期疗效。
Clin Immunol. 2005 Nov;117(2):133-43. doi: 10.1016/j.clim.2005.07.006. Epub 2005 Aug 22.
6
7
T lymphocyte ontogeny in adenosine deaminase-deficient severe combined immune deficiency after treatment with polyethylene glycol-modified adenosine deaminase.聚乙二醇修饰的腺苷脱氨酶治疗后腺苷脱氨酶缺陷型重症联合免疫缺陷中的T淋巴细胞个体发生
J Clin Invest. 1993 Aug;92(2):596-602. doi: 10.1172/JCI116626.
8
Bone marrow transplantation and alternatives for adenosine deaminase deficiency.骨髓移植和替代疗法治疗腺苷脱氨酶缺乏症。
Immunol Allergy Clin North Am. 2010 May;30(2):221-36. doi: 10.1016/j.iac.2010.01.002.
9
Outcomes in two Japanese adenosine deaminase-deficiency patients treated by stem cell gene therapy with no cytoreductive conditioning.两名接受无细胞减灭预处理的干细胞基因治疗的日本腺苷脱氨酶缺乏症患者的结果。
J Clin Immunol. 2015 May;35(4):384-98. doi: 10.1007/s10875-015-0157-1. Epub 2015 Apr 15.
10
Chondroosseous dysplasia in severe combined immunodeficiency due to adenosine deaminase deficiency (chondroosseous dysplasia in ADA deficiency SCID).腺苷脱氨酶缺乏所致重症联合免疫缺陷中的软骨骨发育异常（腺苷脱氨酶缺乏型重症联合免疫缺陷中的软骨骨发育异常）
Pediatr Radiol. 1991;21(6):447-8. doi: 10.1007/BF02026688.
Zotero 插件