Dougherty F E, Ernst S G, Aprille J R
Division of Genetics and Metabolism, Children's Hospital of Boston, Massachusetts 02115.
J Pediatr. 1994 Nov;125(5 Pt 1):758-61. doi: 10.1016/s0022-3476(94)70073-7.
We report a clinically heterogeneous, multigenerational pedigree with the syndrome of mitochondrial encephalomyopathy, lactic acidosis, and stroke-like episodes (MELAS) associated with a mutation at nucleotide 3243 in the mitochondrial DNA tRNA(Leu)(UUR) gene. Our findings suggest that the mutation at nucleotide 3243 is not always associated with the classic MELAS phenotype and that other symptoms (notably cardiac and gastrointestinal abnormalities) should raise the suspicion of a mitochondrial disorder.
我们报告了一个临床异质性的多代家系,其患有与线粒体DNA亮氨酰tRNA(UUR)基因第3243位核苷酸突变相关的线粒体脑肌病、乳酸酸中毒和卒中样发作综合征(MELAS)。我们的研究结果表明,第3243位核苷酸的突变并不总是与经典的MELAS表型相关,其他症状(尤其是心脏和胃肠道异常)应引起对线粒体疾病的怀疑。