Birnbaumer M, Gilbert S, Rosenthal W
Department of Cell Biology, Baylor College of Medicine, Houston, Texas 77030.
Mol Endocrinol. 1994 Jul;8(7):886-94. doi: 10.1210/mend.8.7.7984150.
The mutation of the type-2 vasopressin receptor (V2R) apparently responsible for X-linked congenital nephrogenic diabetes insipidus (CNDI) in the Q3 family consists of a T to C transition in codon 113, causing the change of Arg-113 to Trp. Arg-113 is located in the putative first extracellular loop of the V2R next to a frequently conserved Cys thought to interact via a disulfide bridge with a Cys of the second extracellular loop. The present study explored whether this mutation may account for the CNDI phenotype. The mutation was excised from the genomic DNA of a Q3 patient and introduced into the V2R cDNA, which was then placed into an expression plasmid and transfected into COS cells for transient expression and murine L cells for stable expression. Studies with L cells expressing similar levels of wild type and Q3 receptors showed that the mutant receptor has a 20-fold reduced affinity for arginine vasopressin (AVP) and stimulates adenylyl cyclase with an EC50 that is increased by a factor of about 60-fold. The same shift in the EC50 for adenylyl cyclase stimulation was obtained when deamino[8-D-Arg]vasopressin was substituted for AVP. Studies with COS cells revealed that at equal levels of transfected DNA, the mutant receptor is expressed at lower levels (about 20%) than the wild type receptor, indicating that the mutation hinders the transport of the receptor to the cell membrane.(ABSTRACT TRUNCATED AT 250 WORDS)
在Q3家族中,显然导致X连锁先天性肾性尿崩症(CNDI)的2型血管加压素受体(V2R)突变,是密码子113处的T到C转换,导致精氨酸-113变为色氨酸。精氨酸-113位于V2R假定的第一个细胞外环中,紧邻一个经常保守的半胱氨酸,该半胱氨酸被认为通过二硫键与第二个细胞外环的一个半胱氨酸相互作用。本研究探讨了这种突变是否可以解释CNDI表型。该突变从一名Q3患者的基因组DNA中切除,并引入V2R cDNA,然后将其放入表达质粒中,转染到COS细胞中进行瞬时表达,并转染到小鼠L细胞中进行稳定表达。对表达相似水平野生型和Q3受体的L细胞的研究表明,突变受体对精氨酸血管加压素(AVP)的亲和力降低了20倍,刺激腺苷酸环化酶的EC50增加了约60倍。当用去氨基[8-D-精氨酸]血管加压素替代AVP时,腺苷酸环化酶刺激的EC50也出现了同样的变化。对COS细胞的研究表明,在转染DNA水平相同的情况下,突变受体的表达水平比野生型受体低(约20%),这表明该突变阻碍了受体向细胞膜的转运。(摘要截短于250字)