Girard B, Hoang-Xuan T, D'Hermies F, Savoldelli M, Bennouna M, Poenaru L, Maroteaux P, Pouliquen Y
Service d'Ophtalmologie, Hôpital Robert Ballanger, Aulnaysous-Bois.
J Fr Ophtalmol. 1994;17(4):286-95.
The authors report the case of a 37 year-old male who presented with type I Hurler-Scheie (H-S) mucopolysaccharidosis revealed by ocular complications including bilateral corneal opacification and glaucoma. These complications are identical to those seen in Scheie's mucopolysaccharidosis. The patient underwent a trabeculectomy and a penetrating keratoplasty in both eyes. The corneal storage material was shown on the histological and ultrastructural examination of the buttons. These ocular complications result from excessive tissular storage of acid mucopolysaccharides due to an enzymatic alpha-L-iduronidase deficiency which was proved in our patient. H-S mucopolysaccharidosis is also characterized by dysmorphia and altered intellectual functions like in Hurler's disease in which the prognosis is however. The characteristics of the disease are discussed as well as the different therapeutical strategies which rely on leucocyte injections, skin fibroblast or bone marrow transplantation.
作者报告了一例37岁男性患者,其患有I型Hurler-Scheie(H-S)黏多糖贮积症,表现为眼部并发症,包括双侧角膜混浊和青光眼。这些并发症与Scheie黏多糖贮积症所见的并发症相同。该患者接受了双眼小梁切除术和穿透性角膜移植术。纽扣状角膜组织的组织学和超微结构检查显示了角膜储存物质。这些眼部并发症是由于患者体内α-L-艾杜糖醛酸酶缺乏,导致酸性黏多糖在组织中过度储存所致。H-S黏多糖贮积症也具有畸形和智力功能改变的特点,与Hurler病相似,但其预后有所不同。文中讨论了该疾病的特征以及依赖白细胞注射、皮肤成纤维细胞或骨髓移植的不同治疗策略。