van der Harten H J, Brons J T, Dijkstra P F, Barth P G, Niermeyer M F, Meijer C J, van Geijn H P, Arts N F
Department of Pathology, Free University Hospital, Amsterdam, The Netherlands.
Clin Dysmorphol. 1993 Jan;2(1):1-19.
Data on twenty-two infants with lethal neonatal short-limbed platyspondylic dysplasia are reported. Thanatophoric dysplasia (TD) is the most frequent diagnosis in this group. TD combined with a cloverleaf skull (CS), has been variably classified. TD type 1 with curved femora is rarely combined with CS; TD type 2 with straight femora is almost always associated with CS. Other varieties of TD, known as 'Torrance', 'San Diego' or 'Luton' types, are separate entities. Apart from the differences in radiography and osteochondrohistology, the temporal-lobe abnormalities seen in TD were absent in one of the cases of the 'Torrance' variety. There were also differences in the composition of the cartilage glycosaminoglycans between this case and TD. Nearly all of the cases of these different types mentioned in the literature, including those of this study group, have been sporadic and may result from new dominant mutations. Documentation and classification by full (postmortem) radiography and osteochondrohistology is essential for two reasons. It will be the foundation for the clinical geneticist to inform the parents about the risk of recurrence. It will also be the basis for a biochemical or molecular-biological classification in the near future.
报告了22例患有致死性新生儿短肢扁平脊椎发育不良的婴儿的数据。致死性发育不良(TD)是该组中最常见的诊断。TD合并三叶形颅骨(CS),分类存在差异。股骨弯曲的1型TD很少与CS合并;股骨直的2型TD几乎总是与CS相关。其他类型的TD,如“托伦斯”、“圣地亚哥”或“卢顿”型,是独立的实体。除了放射学和骨软骨组织学的差异外,在“托伦斯”型的一个病例中未发现TD中所见的颞叶异常。该病例与TD之间的软骨糖胺聚糖组成也存在差异。文献中提到的这些不同类型的几乎所有病例,包括本研究组的病例,都是散发性的,可能是新的显性突变导致的。通过完整(尸检)放射学和骨软骨组织学进行记录和分类至关重要,原因有二。这将是临床遗传学家告知父母复发风险的基础。这也将是不久的将来进行生化或分子生物学分类的基础。