Lisziewicz J, Sun D, Gallo R C, Ensoli B, Lori F
Research Institute for Genetic and Human Therapy, Gaithersburg, MD 20879, USA.
Hum Gene Ther. 1996 Dec 1;7(18):2209-16. doi: 10.1089/hum.1996.7.18-2209.
Because human immunodeficiency virus type 1 (HIV-1) infection is characterized by a large number of viral replication cycles and rapid cell turnover in vivo, successful gene therapy requires an approach effective under these conditions. The antitat gene has been proposed for gene therapy because it effectively blocks Tat function and the replication of HIV-1. However, neither antitat nor any other antiviral gene has been shown to inhibit HIV in the presence of high viral load and inflammatory cytokines, a condition closer to the in vivo situation. We show that cells transduced with antitat retrovirus vector are resistant to high multiplicity of HIV infection. In the presence of inflammatory cytokines, including interleukin-1 and tumor necrosis factor, both known to activate viral gene expression independently of Tat, antitat suppressed virus replication. HIV-1 inhibition was observed when cell were treated with a mixture of inflammatory cytokines able to induce acquired immunodeficiency syndrome (AIDS) Kaposi's sarcoma cell growth. These molecules have been shown to be increased in HIV-1-infected individuals, and it is suggested they play a role in the pathogenesis of AIDS. Our results suggest that antitat is effective under conditions present in vivo and therefore a primary candidate for HIV-1 gene therapy.
由于1型人类免疫缺陷病毒(HIV-1)感染的特点是体内存在大量病毒复制周期且细胞更新迅速,因此成功的基因治疗需要一种在这些条件下有效的方法。抗Tat基因已被提议用于基因治疗,因为它能有效阻断Tat功能及HIV-1的复制。然而,在高病毒载量和炎性细胞因子存在的情况下(这种情况更接近体内实际情况),抗Tat基因以及任何其他抗病毒基因均未显示出能抑制HIV。我们发现,用抗Tat逆转录病毒载体转导的细胞对高感染复数的HIV感染具有抗性。在炎性细胞因子(包括已知可独立于Tat激活病毒基因表达的白细胞介素-1和肿瘤坏死因子)存在的情况下,抗Tat基因可抑制病毒复制。当用能够诱导获得性免疫缺陷综合征(AIDS)卡波西肉瘤细胞生长的炎性细胞因子混合物处理细胞时,可观察到HIV-1受到抑制。这些分子在HIV-1感染个体中已被证明会增加,提示它们在AIDS发病机制中起作用。我们的结果表明,抗Tat基因在体内存在的条件下是有效的,因此是HIV-1基因治疗的主要候选基因。