Adeokun A M, West S P, Ellis F R, Halsall P J, Hopkins P M, Foroughmand A M, Iles D E, Robinson R L, Stewart A D, Curran J L
Department of Human Genetics, University of Newcastle upon Tyne, United Kingdom.
Am J Hum Genet. 1997 Apr;60(4):833-41.
A single base change in the RYR1 gene encoding the skeletal muscle ryanodine receptor (calcium-sensitive calcium-release channel of the sarcoplasmic reticulum), resulting in the substitution of G1021 by A, has been proposed to underlie malignant-hyperthermia (MH) susceptibility in as many as 10% of cases in the European population. As part of our mutation-screening program in MH-susceptible (MHS) individuals, we have investigated this substitution in individuals from 151 unrelated British MHS families and have detected G1021A heterozygotes in 7 families. This mutation was not found in 156 unrelated MH-negative (MHN) individuals. We also examined eight families with central core disease (CCD): the mutation did not occur in any family members of any disease status (affected or unaffected for CCD, MHS, or MHN). In one large family, the G1021A mutation was found but did not show complete cosegregation with MH susceptibility: it occurred in only 7/12 MHS individuals in the kinship, and susceptibility was inherited from parents who were G1021 homozygotes, as well as from parents who were heterozygotes. On the basis of these findings, it is clearly unreliable at present to offer presymptomatic DNA testing for MH status, even in families in which a mutation has been detected.
编码骨骼肌兰尼碱受体(肌浆网的钙敏感钙释放通道)的RYR1基因中的单个碱基变化,导致G1021被A取代,有人提出这是欧洲人群中多达10%的恶性高热(MH)易感性的基础。作为我们对MH易感(MHS)个体进行突变筛查项目的一部分,我们对来自151个不相关的英国MHS家庭的个体进行了这一替代位点的研究,在7个家庭中检测到了G1021A杂合子。在156个不相关的MH阴性(MHN)个体中未发现该突变。我们还检查了8个患有中央轴空病(CCD)的家庭:在任何疾病状态(CCD、MHS或MHN的患病或未患病)的家庭成员中均未出现该突变。在一个大家庭中,发现了G1021A突变,但它与MH易感性并未完全共分离:在该亲属关系中的12个MHS个体中,只有7个出现了该突变,并且易感性是从G1021纯合子的父母以及杂合子的父母那里遗传而来的。基于这些发现,目前即使在已检测到突变的家庭中,提供针对MH状态的症状前DNA检测显然也是不可靠的。