Senut M C, Suhr S T, Gage F H
Laboratory of Genetics, The Salk Institute for Biological Studies, La Jolla, California 92037, USA.
J Clin Invest. 1998 Apr 15;101(8):1565-71. doi: 10.1172/JCI1959.
The delivery of biologically active factors to the developing mammalian embryo by in utero gene transfer has generated considerable interest but limited success. The chorioallantoic placenta is a potential alternative target for providing therapeutic transgenes to the fetus during gestation. We demonstrate that somatic gene transfer to the midgestation rat placenta may be efficiently accomplished in situ through the implantation of a variety of genetically modified cells with different antigenic and growth properties. Ex vivo-modified cells survived and retained transgene expression until term. Proteins secreted from the transplanted cells were detectable within the fetal trunk blood. These studies suggest that gene transfer to the placenta may be a useful tool for answering questions of both embryonic and placental development and providing therapeutic proteins during gestation for amelioration of diseases with onset during embryonic life.
通过子宫内基因转移将生物活性因子传递给发育中的哺乳动物胚胎已引起了广泛关注,但取得的成功有限。绒毛膜尿囊胎盘是在妊娠期间为胎儿提供治疗性转基因的潜在替代靶点。我们证明,通过植入具有不同抗原和生长特性的多种基因修饰细胞,可以在原位有效地将体细胞基因转移到妊娠中期大鼠胎盘。经体外修饰的细胞存活并保留转基因表达直至足月。在胎儿躯干血液中可检测到移植细胞分泌的蛋白质。这些研究表明,向胎盘进行基因转移可能是一个有用的工具,可用于解答胚胎和胎盘发育问题,并在妊娠期间提供治疗性蛋白质,以改善胚胎期发病的疾病。