Haass C, Grünberg J, Capell A, Wild-Bode C, Leimer U, Walter J, Yamazaki T, Ihara I, Zweckbronner I, Jakubek C, Baumeister R
Central Institute for Mental Health, Department of Molecular Biology, Mannheim, Federal Republic of Germany.
J Neural Transm Suppl. 1998;53:159-67. doi: 10.1007/978-3-7091-6467-9_14.
Amyloid beta-peptide (A beta), the major component of senile plaques, is generated by proteolytic processing from the beta-amyloid precursor protein (beta APP). Mutations within the beta APP gene cause early onset familial AD (FAD) by affecting A beta generation. Interestingly, the much more abundant mutations within the presenilin (PS) genes also result in the abnormal generation of a 42 residue A beta (A beta 42), thus clearly supporting a pivotal role of A beta for the pathology of AD. PS proteins are proteolytically processed into stable 30 kDa N-terminal fragments (NTF) and 20 kDa C-terminal fragments (CTF). Beside the conventional proteolytic pathway. PS proteins can also be cleaved further C-terminal by proteases of the caspase superfamily. PS proteins were localized within the endoplasmic reticulum (ER) and early Golgi, compartments which we have demonstrated to be involved in A beta 42 generation and intracellular accumulation. Using Caenorhabditis elegans as a simple animal model, we demonstrate that PS proteins are involved in NOTCH signaling FAD causing mutations interfere with the biological function of PS proteins in NOTCH signaling.
淀粉样β肽(Aβ)是老年斑的主要成分,由β淀粉样前体蛋白(βAPP)经蛋白水解加工产生。βAPP基因内的突变通过影响Aβ的产生导致早发性家族性阿尔茨海默病(FAD)。有趣的是,早老素(PS)基因中更为常见的突变也会导致42个残基的Aβ(Aβ42)异常产生,从而明确支持了Aβ在阿尔茨海默病病理过程中的关键作用。PS蛋白经蛋白水解加工形成稳定的30 kDa N端片段(NTF)和20 kDa C端片段(CTF)。除了传统的蛋白水解途径外,PS蛋白还可被半胱天冬酶超家族的蛋白酶进一步在C端切割。PS蛋白定位于内质网(ER)和早期高尔基体,我们已证明这些区室参与Aβ42的产生和细胞内积累。利用秀丽隐杆线虫作为简单的动物模型,我们证明PS蛋白参与NOTCH信号传导,导致FAD的突变会干扰PS蛋白在NOTCH信号传导中的生物学功能。