Svensson P J, Molander M L, Eng C, Anvret M, Nordenskjöld A
Department of Molecular Medicine, Karolinska Hospital, Stockholm, Sweden.
Clin Genet. 1998 Jul;54(1):39-44. doi: 10.1111/j.1399-0004.1998.tb03691.x.
Hirschsprung disease is a congenital malformation, where absence of intramural ganglia in the hindgut results in a defect in the coordination of peristaltic movement. This leads to ileus in the newborn or, more often, constipation in children and adults. The disease affects one in 5000 live births. Siblings of affected cases are at an increased risk (4%) of developing the disease. Among cases. males are affected more often than females. The first major susceptibility gene for Hirschsprung disease is the RET proto-oncogene on 10q11.2. Germline RET mutations in Hirschsprung disease are mainly inactivating, and have been reported to account for up to 20 and 50% of sporadic and familial cases, respectively. We have screened Swedish population-based samples from 62 sporadic cases and seven familial cases of Hirschsprung disease with single strand conformation polymorphism (SSCP), and found five mutations.
先天性巨结肠症是一种先天性畸形,后肠壁内神经节缺失导致蠕动运动协调缺陷。这会导致新生儿肠梗阻,或更常见的是儿童及成人便秘。该疾病在每5000例活产中出现1例。患病病例的兄弟姐妹患该病的风险增加(4%)。在病例中,男性比女性更常受影响。先天性巨结肠症的首个主要易感基因是位于10q11.2的RET原癌基因。先天性巨结肠症中的种系RET突变主要是失活突变,据报道分别占散发性和家族性病例的20%和50%。我们用单链构象多态性(SSCP)对来自62例散发性先天性巨结肠症病例和7例家族性病例的瑞典人群样本进行了筛查,发现了5个突变。