Peoples R, Franke Y, Wang Y K, Pérez-Jurado L, Paperna T, Cisco M, Francke U
Department of Genetics, Stanford University School of Medicine, Stanford, CA, USA.
Am J Hum Genet. 2000 Jan;66(1):47-68. doi: 10.1086/302722.
Williams-Beuren syndrome (WBS) is a developmental disorder caused by haploinsufficiency for genes in a 2-cM region of chromosome band 7q11.23. With the exception of vascular stenoses due to deletion of the elastin gene, the various features of WBS have not yet been attributed to specific genes. Although >/=16 genes have been identified within the WBS deletion, completion of a physical map of the region has been difficult because of the large duplicated regions flanking the deletion. We present a physical map of the WBS deletion and flanking regions, based on assembly of a bacterial artificial chromosome/P1-derived artificial chromosome contig, analysis of high-throughput genome-sequence data, and long-range restriction mapping of genomic and cloned DNA by pulsed-field gel electrophoresis. Our map encompasses 3 Mb, including 1.6 Mb within the deletion. Two large duplicons, flanking the deletion, of >/=320 kb contain unique sequence elements from the internal border regions of the deletion, such as sequences from GTF2I (telomeric) and FKBP6 (centromeric). A third copy of this duplicon exists in inverted orientation distal to the telomeric flanking one. These duplicons show stronger sequence conservation with regard to each other than to the presumptive ancestral loci within the common deletion region. Sequence elements originating from beyond 7q11.23 are also present in these duplicons. Although the duplicons are not present in mice, the order of the single-copy genes in the conserved syntenic region of mouse chromosome 5 is inverted relative to the human map. A model is presented for a mechanism of WBS-deletion formation, based on the orientation of duplicons' components relative to each other and to the ancestral elements within the deletion region.
威廉姆斯-贝伦综合征(WBS)是一种发育障碍,由染色体7q11.23带2厘摩区域内基因的单倍剂量不足引起。除了因弹力蛋白基因缺失导致的血管狭窄外,WBS的各种特征尚未归因于特定基因。尽管在WBS缺失区域内已鉴定出≥16个基因,但由于缺失侧翼存在大量重复区域,该区域物理图谱的绘制一直很困难。我们基于细菌人工染色体/P1衍生人工染色体重叠群的组装、高通量基因组序列数据的分析以及通过脉冲场凝胶电泳对基因组和克隆DNA进行的长距离限制性图谱分析,展示了WBS缺失区域及其侧翼区域的物理图谱。我们的图谱涵盖3兆碱基,其中包括缺失区域内的1.6兆碱基。缺失侧翼的两个≥320千碱基的大型重复子包含来自缺失内部边界区域的独特序列元件,如来自GTF2I(端粒)和FKBP6(着丝粒)的序列。该重复子的第三个拷贝以反向排列存在于端粒侧翼重复子的远端。这些重复子彼此之间的序列保守性比与共同缺失区域内的推定祖先基因座更强。这些重复子中也存在源自染色体7q11.23以外区域的序列元件。尽管小鼠中不存在这些重复子,但小鼠染色体5保守同线区域中单拷贝基因的顺序与人图谱相比是颠倒的。基于重复子元件相对于彼此以及相对于缺失区域内祖先元件的方向,提出了一种WBS缺失形成机制的模型。