Bichet D G, Hendy G N, Lonergan M, Arthus M F, Ligier S, Pausova Z, Kluge R, Zingg H, Saenger P, Oppenheimer E
Département de Médecine, Hôpital du Sacré-Coeur, Université de Montréal, Québec, Canada.
Am J Hum Genet. 1992 Nov;51(5):1089-1102.
Nephrogenic diabetes insipidus (NDI; designated 304800 in Mendelian Inheritance in Man) is an X-linked disorder with abnormal renal and extrarenal V2 vasopressin receptor responses. The mutant gene has been mapped to Xq28 by analysis of RFLPs, and tight linkage between DXS52 and NDI has been reported. In 1969, Bode and Crawford proposed, under the term "the Hopewell hypothesis," that most cases in North America could be traced to descendants of Ulster Scots who arrived in Nova Scotia in 1761 on the ship Hopewell. They also suggested a link between this family and a large Mormon pedigree. DNA samples obtained from 13 independent affected families, including 42 members of the Hopewell and Mormon pedigrees, were analyzed with probes in the Xq28 region. Genealogical reconstructions were performed. Linkage between NDI and DXS304 (probe U6:2.spl), DXS305 (St35-691), DXS52 (St14-1), DXS15 (DX13), and F8C (F814) showed no recombination in 12 families, with a maximum lod score of 13.5 for DXS52. A recombinant between NDI and DXS304, DXS305, was identified in one family. The haplotype segregating with the disease in the Hopewell pedigree was not shared by other North American families. PCR analysis of the St14 VNTR allowed the distinction of two alleles that were not distinguishable by Southern analysis. Carrier status was predicted in 24 of 26 at-risk females. The Hopewell hypothesis cannot explain the origin of NDI in many of the North American families, since they have no apparent relationship with the Hopewell early settlers, either by haplotype or by genealogical analysis. We confirm the locus homogeneity of the disease by linkage analysis in ethnically diverse families. PCR analysis of the DXS52 VNTR in NDI families is very useful for carrier testing and presymptomatic diagnosis, which can prevent the first manifestations of dehydration.
肾性尿崩症(NDI;在《人类孟德尔遗传》中编号为304800)是一种X连锁疾病,其肾脏和肾外V2血管加压素受体反应异常。通过对限制性片段长度多态性(RFLP)的分析,已将突变基因定位到Xq28,并且有报道称DXS52与NDI之间存在紧密连锁。1969年,博德和克劳福德在“霍普韦尔假说”这一术语下提出,北美大多数病例可追溯到1761年乘坐“霍普韦尔号”船抵达新斯科舍的阿尔斯特苏格兰人的后裔。他们还提出了这个家族与一个大型摩门教谱系之间的联系。使用Xq28区域的探针分析了从13个独立的患病家族获取的DNA样本,其中包括霍普韦尔和摩门教谱系的42名成员。进行了系谱重建。NDI与DXS304(探针U6:2.spl)、DXS305(St35 - 691)、DXS52(St14 - 1)、DXS15(DX13)和F8C(F814)之间的连锁分析显示,在12个家族中没有重组,DXS52的最大对数优势分数为13.5。在一个家族中鉴定出NDI与DXS304、DXS305之间的一个重组体。霍普韦尔谱系中与疾病分离的单倍型未被其他北美家族共享。对St14可变数目串联重复序列(VNTR)的聚合酶链反应(PCR)分析能够区分两个通过Southern分析无法区分的等位基因。在26名有风险的女性中,预测出了24名携带者状态。霍普韦尔假说无法解释许多北美家族中NDI的起源,因为无论是通过单倍型还是系谱分析,他们与霍普韦尔早期定居者都没有明显的关系。我们通过对不同种族家族的连锁分析证实了该疾病的基因座同质性。对NDI家族中DXS52 VNTR的PCR分析对于携带者检测和症状前诊断非常有用,这可以预防脱水的首次表现。