Safley Anne Michele, Sebastian Siby, Collins Timothy S, Tirado Carlos A, Stenzel Timothy T, Gong Jerald Z, Goodman Barbara K
Duke University School of Medicine, Durham, NC 27710, USA.
Genes Chromosomes Cancer. 2004 May;40(1):44-50. doi: 10.1002/gcc.20014.
We report a case of BCR-ABL-negative atypical chronic myeloid leukemia (CML) with translocation t(4;22) (q12;q11.2) juxtaposing the breakpoint cluster region (BCR) and platelet-derived growth factor receptor-alpha (PDGFRA) genes. The patient was a 57-year-old man with a history of stage IV diffuse large B-cell lymphoma, status post-6 cycles of combination chemotherapy in 1999, who presented in August 2002 with enlarged lymph nodes, anemia, and marked leukocytosis (50 x 10(9) g/dL) consistent with a myeloproliferative disorder (MPD). A bone marrow biopsy showed granulocytic hyperplasia, neutrophilia, and mild eosinophilia. Initial cytogenetic evaluation by interphase FISH for BCR-ABL, to rule out a translocation 9;22, showed a variant signal pattern consistent with rearrangement of BCR at 22q11.2, but not ABL at 9q34. Analysis of the patient's cDNA by polymerase chain reaction (PCR) for BCR-ABL was negative. Cytogenetic analysis showed an abnormal karyotype with rearrangement of chromosomes 4 and 22. PCR amplification and subsequent sequence analysis demonstrated an in-frame 5'-BCR/3'-PDGFRA fusion in the patient's cDNA. PDGFRA encodes a receptor tyrosine kinase and shares structural and organizational homology with the KIT and CSf1R receptor genes. However, although the incidence of MPD involving translocations of PDGFRB has been well established, to our knowledge there are only two previous reports describing a BCR-PDGFRA fusion gene, in 3 patients diagnosed with atypical CML. Here, we report the molecular and cytogenetic characterization of a patient with BCR-PDGFRA-positive MPD who had a complete hematologic response after treatment with imatinib mesylate.
我们报告一例BCR-ABL阴性的非典型慢性髓性白血病(CML),其发生t(4;22)(q12;q11.2)易位,使断裂点簇集区(BCR)基因与血小板衍生生长因子受体α(PDGFRA)基因并列。患者为一名57岁男性,有IV期弥漫性大B细胞淋巴瘤病史,1999年接受了6周期联合化疗,2002年8月出现淋巴结肿大、贫血和明显的白细胞增多(50×10⁹/L),符合骨髓增殖性疾病(MPD)。骨髓活检显示粒细胞增生、中性粒细胞增多和轻度嗜酸性粒细胞增多。通过间期荧光原位杂交(FISH)对BCR-ABL进行初步细胞遗传学评估以排除9;22易位,结果显示一种变异信号模式,与22q11.2处的BCR重排一致,但9q34处的ABL无重排。通过聚合酶链反应(PCR)对患者cDNA进行BCR-ABL分析为阴性。细胞遗传学分析显示异常核型,4号和22号染色体重排。PCR扩增及随后的序列分析证实患者cDNA中存在框内5'-BCR/3'-PDGFRA融合。PDGFRA编码一种受体酪氨酸激酶,与KIT和CSf1R受体基因具有结构和组织同源性。然而,尽管涉及PDGFRB易位的MPD发病率已得到充分证实,但据我们所知,此前仅有两篇报道描述了3例诊断为非典型CML患者中的BCR-PDGFRA融合基因。在此,我们报告一例BCR-PDGFRA阳性MPD患者的分子和细胞遗传学特征,该患者接受甲磺酸伊马替尼治疗后获得完全血液学缓解。