von Levetzow Gregor, Spanholtz Jan, Beckmann Julia, Fischer Johannes, Kögler Gesine, Wernet Peter, Punzel Michael, Giebel Bernd
Institute for Transplantation Diagnostics and Cell Therapeutics, Heinrich-Heine-University Düsseldorf, D-40225 Düsseldorf, Germany.
Stem Cells Dev. 2006 Apr;15(2):278-85. doi: 10.1089/scd.2006.15.278.
The targeted manipulation of the genetic program of single cells as well as of complete organisms has strongly enhanced our understanding of cellular and developmental processes and should also help to increase our knowledge of primary human stem cells, e.g., hematopoietic stem cells (HSCs), within the next few years. An essential requirement for such genetic approaches is the existence of a reliable and efficient method to introduce genetic elements into living cells. Retro- and lentiviral techniques are efficient in transducing primary human HSCs, but remain labor and time consuming and require special safety conditions, which do not exist in many laboratories. In our study, we have optimized the nucleofection technology, a modified electroporation strategy, to introduce plasmid DNA into freshly isolated human HSC-enriched CD34(+) cells. Using enhanced green fluorescent protein (eGFP)-encoding plasmids, we obtained transfection efficiencies of approximately 80% and a mean survival rate of 50%. Performing functional assays using GFU-GEMM and long-term culture initiating cells (LTC-IC), we demonstrate that apart from a reduction in the survival rate the nucleofection method itself does not recognizably change the short- or long-term cell fate of primitive hematopoietic cells. Therefore, we conclude, the nucleofection method is a reliable and efficient method to manipulate primitive hematopoietic cells genetically.
对单细胞以及完整生物体的遗传程序进行靶向操作,极大地增进了我们对细胞和发育过程的理解,并且在未来几年内也应有助于增加我们对人类原代干细胞(例如造血干细胞(HSC))的了解。此类遗传方法的一个基本要求是存在一种可靠且高效的将遗传元件导入活细胞的方法。逆转录病毒和慢病毒技术在转导人类原代造血干细胞方面是有效的,但仍然耗时费力,并且需要特殊的安全条件,而许多实验室并不具备这些条件。在我们的研究中,我们优化了核转染技术(一种改良的电穿孔策略),以将质粒DNA导入新鲜分离的富含人类造血干细胞的CD34(+)细胞中。使用编码增强型绿色荧光蛋白(eGFP)的质粒,我们获得了约80%的转染效率和50%的平均存活率。通过使用粒-巨噬细胞集落形成单位(GFU-GEMM)和长期培养起始细胞(LTC-IC)进行功能测定,我们证明除了存活率降低外,核转染方法本身并不会明显改变原始造血细胞的短期或长期细胞命运。因此,我们得出结论,核转染方法是一种可靠且高效的对原始造血细胞进行基因操作的方法。