Rooryck C, Pelras S, Chateil J-F, Cances C, Arveiler B, Verloes A, Lacombe D, Goizet C
Service de Génétique Médicale, CHU Pellegrin-Enfants, Bordeaux, France.
Neuropediatrics. 2007 Feb;38(1):5-9. doi: 10.1055/s-2007-981466.
Bardet-Biedl syndrome (BBS) is a rare autosomal recessive disorder with clinical and genetic heterogeneity. The main features are obesity, polydactyly, pigmentary retinopathy, learning disabilities, hypogonadism, and renal abnormalities. To date, eleven genes have been cloned but there is still little knowledge about genotype/phenotype correlations. We describe three additional cases with BBS and cerebral abnormalities and focus on cerebellar abnormalities in BBS.
巴德-比德尔综合征(BBS)是一种罕见的常染色体隐性疾病,具有临床和遗传异质性。主要特征包括肥胖、多指(趾)畸形、色素性视网膜病变、学习障碍、性腺功能减退和肾脏异常。迄今为止,已有11个基因被克隆,但关于基因型/表型相关性的了解仍然很少。我们描述了另外3例患有BBS和脑部异常的病例,并重点关注BBS中的小脑异常。