Jones Siân, Hruban Ralph H, Kamiyama Mihoko, Borges Michael, Zhang Xiaosong, Parsons D Williams, Lin Jimmy Cheng-Ho, Palmisano Emily, Brune Kieran, Jaffee Elizabeth M, Iacobuzio-Donahue Christine A, Maitra Anirban, Parmigiani Giovanni, Kern Scott E, Velculescu Victor E, Kinzler Kenneth W, Vogelstein Bert, Eshleman James R, Goggins Michael, Klein Alison P
Ludwig Center for Cancer Genetics and Therapeutics and Howard Hughes Medical Institute, Baltimore, MD 21231, USA.
Science. 2009 Apr 10;324(5924):217. doi: 10.1126/science.1171202. Epub 2009 Mar 5.
Through complete sequencing of the protein-coding genes in a patient with familial pancreatic cancer, we identified a germline, truncating mutation in PALB2 that appeared responsible for this patient's predisposition to the disease. Analysis of 96 additional patients with familial pancreatic cancer revealed three distinct protein-truncating mutations, thereby validating the role of PALB2 as a susceptibility gene for pancreatic cancer. PALB2 mutations have been previously reported in patients with familial breast cancer, and the PALB2 protein is a binding partner for BRCA2. These results illustrate that complete, unbiased sequencing of protein-coding genes can lead to the identification of a gene responsible for a hereditary disease.
通过对一名家族性胰腺癌患者的蛋白质编码基因进行全测序,我们在PALB2基因中发现了一个种系截短突变,该突变似乎是导致该患者易患此病的原因。对另外96名家族性胰腺癌患者的分析发现了三种不同的蛋白质截短突变,从而证实了PALB2作为胰腺癌易感基因的作用。此前在家族性乳腺癌患者中也报道过PALB2突变,并且PALB2蛋白是BRCA2的结合伴侣。这些结果表明,对蛋白质编码基因进行完整、无偏倚的测序能够鉴定出导致一种遗传性疾病的基因。