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Chemotherapy is successful in sporadic late onset nemaline myopathy (SLONM) with monoclonal gammopathy.

作者信息

Novy Jan, Rosselet Anne, Spertini Olivier, Lobrinus Johannes Alexander, Pabst Thomas, Kuntzer Thierry

出版信息

Muscle Nerve. 2010 Feb;41(2):286-7. doi: 10.1002/mus.21560.

DOI:10.1002/mus.21560
PMID:19918772
Abstract
摘要

相似文献

1
Chemotherapy is successful in sporadic late onset nemaline myopathy (SLONM) with monoclonal gammopathy.化疗对伴有单克隆丙种球蛋白病的散发性晚发型杆状体肌病(SLONM)有效。
Muscle Nerve. 2010 Feb;41(2):286-7. doi: 10.1002/mus.21560.
2
Sporadic late onset nemaline myopathy responsive to IVIg and immunotherapy.散发性迟发性杆状体肌病对 IVIg 和免疫疗法有反应。
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3
Sporadic late-onset nemaline myopathy with monoclonal gammopathy of undetermined significance (SLONM-MGUS): An alternative treatment using cyclophosphamide-thalidomide-dexamethasone (CTD) regimen.散发型迟发性肌病伴意义未明的单克隆丙种球蛋白血症(SLONM-MGUS):使用环磷酰胺-沙利度胺-地塞米松(CTD)方案的一种替代治疗方法。
Neuromuscul Disord. 2018 Jul;28(7):610-613. doi: 10.1016/j.nmd.2018.04.011. Epub 2018 May 16.
4
Sporadic late-onset nemaline myopathy with MGUS: long-term follow-up after melphalan and SCT.散发型迟发性杆状体肌病伴 MGUS:马法兰和 SCT 后的长期随访。
Neurology. 2014 Dec 2;83(23):2133-9. doi: 10.1212/WNL.0000000000001047. Epub 2014 Nov 5.
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Sporadic late-onset nemaline myopathy as a rare cause of slowly progressive muscle weakness with young adult onset.散发性迟发性杆状体肌病是年轻成人起病的缓慢进行性肌肉无力的罕见病因。
Muscle Nerve. 2015 May;51(5):772-4. doi: 10.1002/mus.24509. Epub 2015 Jan 16.
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Sporadic late onset nemaline myopathy.散发性晚发型杆状体肌病
Neurology. 2005 Oct 25;65(8):1158-64. doi: 10.1212/01.wnl.0000180362.90078.dc. Epub 2005 Sep 7.
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Inflammatory features in sporadic late-onset nemaline myopathy are independent from monoclonal gammopathy.散发性晚发性杆状体肌病的炎症特征与单克隆丙种球蛋白无关。
Brain Pathol. 2021 May;31(3):e12962. doi: 10.1111/bpa.12962.
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Sporadic late-onset nemaline myopathy effectively treated by melphalan and stem cell transplant.美法仑和干细胞移植有效治疗散发性迟发性杆状体肌病。
Neurology. 2008 Aug 12;71(7):532-4. doi: 10.1212/01.wnl.0000310814.54623.6f. Epub 2008 Jun 18.
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Adult-onset nemaline myopathy and monoclonal gammopathy: a case report.成人起病的杆状体肌病与单克隆丙种球蛋白病:一例报告。
Acta Neurol Belg. 2000 Mar;100(1):34-40.
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Sporadic late onset nemaline myopathy and immunoglobulin deposition disease.散发性迟发性杆状体肌病和免疫球蛋白沉积病。
Muscle Nerve. 2013 Dec;48(6):983-8. doi: 10.1002/mus.23954. Epub 2013 Oct 28.

引用本文的文献

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Sporadic Late-Onset Nemaline Myopathy: Current Landscape.散发性迟发性杆状体肌病:现状。
Curr Neurol Neurosci Rep. 2023 Nov;23(11):777-784. doi: 10.1007/s11910-023-01311-0. Epub 2023 Oct 19.
2
Impact of hematologic complete response in the treatment of sporadic late-onset nemaline myopathy associated with monoclonal gammopathy.血液学完全缓解在与单克隆丙种球蛋白病相关的散发性迟发性杆状体肌病治疗中的影响
Clin Case Rep. 2021 Jul 16;9(7):e04471. doi: 10.1002/ccr3.4471. eCollection 2021 Jul.
3
Inflammatory features in sporadic late-onset nemaline myopathy are independent from monoclonal gammopathy.
散发性晚发性杆状体肌病的炎症特征与单克隆丙种球蛋白无关。
Brain Pathol. 2021 May;31(3):e12962. doi: 10.1111/bpa.12962.
4
Sporadic late onset nemaline myopathy with monoclonal gammopathy of undetermined significance: two cases with long term stability.散发型迟发性杆状体肌病合并意义未明的单克隆丙种球蛋白病:两例长期病情稳定的病例
Eur J Transl Myol. 2020 Sep 16;30(3):9225. doi: 10.4081/ejtm.2020.9225. eCollection 2020 Sep 30.
5
Chemotherapy with stem cell transplantation is more effective than immunotherapy in sporadic late onset nemaline myopathy with monoclonal gammopathy.对于伴有单克隆丙种球蛋白病的散发性晚发型杆状体肌病,化疗联合干细胞移植比免疫疗法更有效。
Bone Marrow Transplant. 2018 Jul;53(7):895-899. doi: 10.1038/s41409-017-0080-6. Epub 2018 Jan 24.
6
Sporadic late-onset nemaline myopathy: clinical, pathology and imaging findings in a single center cohort.散发性迟发性杆状体肌病:单中心队列的临床、病理和影像学发现。
J Neurol. 2018 Mar;265(3):542-551. doi: 10.1007/s00415-018-8741-y. Epub 2018 Jan 22.
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Sporadic late-onset nemaline myopathy: clinico-pathological characteristics and review of 76 cases.散发性迟发性杆状体肌病:76例临床病理特征及文献复习
Orphanet J Rare Dis. 2017 May 11;12(1):86. doi: 10.1186/s13023-017-0640-2.
8
[Treatability of sporadic late onset nemaline myopathy].
Nervenarzt. 2013 Aug;84(8):955-61. doi: 10.1007/s00115-013-3825-5.
9
Consensus statement on standard of care for congenital myopathies.先天性肌病护理标准的共识声明。
J Child Neurol. 2012 Mar;27(3):363-82. doi: 10.1177/0883073812436605.
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HIV-related neuromuscular diseases: nemaline myopathy, amyotrophic lateral sclerosis and bibrachial amyotrophic diplegia.与艾滋病病毒相关的神经肌肉疾病:杆状体肌病、肌萎缩侧索硬化症和双臂肌萎缩性双侧瘫。
Acta Myol. 2011 Jun;30(1):29-31.