Exon skipping with morpholino oligomers: new treatment option for cardiomyopathy in Duchenne muscular dystrophy?
作者信息
Bauer Ralf, Katus Hugo A, Müller Oliver J
出版信息
Cardiovasc Res. 2010 Feb 1;85(3):409-10. doi: 10.1093/cvr/cvp397. Epub 2009 Dec 14.
PMID:20008475
Abstract
摘要
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Exon skipping with morpholino oligomers: new treatment option for cardiomyopathy in Duchenne muscular dystrophy?使用吗啉代寡聚物进行外显子跳跃：杜氏肌营养不良症心肌病的新治疗选择？
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