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Orphan drug pricing may warrant a competition law investigation.

作者信息

Roos Jonathan C P, Hyry Hanna I, Cox Timothy M

机构信息

Department of Medicine, University of Cambridge, Cambridge CB2 2QQ, UK.

出版信息

BMJ. 2010 Nov 16;341:c6471. doi: 10.1136/bmj.c6471.

DOI:10.1136/bmj.c6471
PMID:21081598
Abstract
摘要

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Orphan drug pricing may warrant a competition law investigation.孤儿药定价可能需要进行竞争法调查。
BMJ. 2010 Nov 16;341:c6471. doi: 10.1136/bmj.c6471.
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The Orphan Drug Act: an engine of innovation? At what cost?《孤儿药法案》:创新的引擎?代价几何?
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[Drugs for rare diseases].[用于罕见病的药物]
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Debates over orphan drug pricing: a meta-narrative literature review.关于罕见病药物定价的争论:一项元叙事文献综述
Orphanet J Rare Dis. 2025 Mar 7;20(1):107. doi: 10.1186/s13023-025-03634-2.
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How Can We Optimize the Value Assessment and Appraisal of Orphan Drugs for Reimbursement Purposes? A Qualitative Interview Study Across European Countries.我们如何优化用于报销目的的罕见病药物价值评估和评价?一项对欧洲国家的定性访谈研究。
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罕见病药物专利、孤儿药认定、授权及收益的动态变化:依库珠单抗的市场拓展
PLoS One. 2021 Mar 5;16(3):e0247853. doi: 10.1371/journal.pone.0247853. eCollection 2021.
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Global research on Fabry's disease: Demands for a rare disease.法布里病的全球研究:对罕见病的需求。
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Oncology drugs for orphan indications: how are HTA processes evolving for this specific drug category?用于罕见病适应症的肿瘤药物:针对这一特定药物类别,卫生技术评估流程是如何演变的?
Clinicoecon Outcomes Res. 2017 Jun 10;9:327-342. doi: 10.2147/CEOR.S134230. eCollection 2017.
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Determinants of orphan drugs prices in France: a regression analysis.法国孤儿药价格的决定因素:一项回归分析。
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Compassionate use of orphan drugs.罕见病药物的同情用药。
Orphanet J Rare Dis. 2015 Aug 21;10:100. doi: 10.1186/s13023-015-0306-x.
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Principles for consistent value assessment and sustainable funding of orphan drugs in Europe.欧洲罕见病药物一致性价值评估及可持续资金投入原则
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