Department of Biotechnology, Graduate School of Engineering, Nagoya University, Furo-cho, Chikusa-ku, Nagoya, 464-8603, Japan.
Transgenic Res. 2012 Feb;21(1):63-75. doi: 10.1007/s11248-011-9511-0. Epub 2011 Apr 13.
As a tool for large scale production of recombinant proteins, chickens have advantages such as high productivity and low breeding costs compared to other animals. We previously reported the production of erythropoietin, the tumor necrosis factor receptor fused to an Fc fragment, and an Fc-fused single-chain Fv antibody in eggs laid by genetically manipulated chickens. In egg white, however, the incomplete addition of terminal sugars such as sialic acid and galactose was found on N-linked glycans of exogenously expressed proteins. This could be a draw back to the use of transgenic chickens since the loss of these terminal sugars may affect the functions and stability of recombinant proteins purified from chicken egg white for pharmaceutical usage. To overcome this problem, we studied galactosyltransferase (GalT) activity in the magnum where the majority of egg-white proteins are secreted. In the magnum, lower β1,4-GalT1 expression and poor galactose-transfer activity were observed. Thus, we supposed that the lack of GalT1 activity may partly cause the incomplete glycosylation of egg-white proteins, and generated genetically manipulated chickens expressing GalT1 by retrovirus-mediated gene transfer. In a Golgi fraction prepared from magnum cells of the genetically manipulated chickens, significant GalT activity was detected. The series of analyses revealed a considerable improvement in the galactosylation of native egg-white proteins as well as an exogenously expressed single-chain Fv antibody fused to an Fc fragment. We conclude that chickens with genetically modified GalT activity in the magnum could be an attractive platform for producing galactosylated therapeutics.
作为大规模生产重组蛋白的工具,与其他动物相比,鸡具有生产效率高和养殖成本低的优势。我们之前曾报道过在经过基因改造的鸡所产的鸡蛋中生产红细胞生成素、与 Fc 片段融合的肿瘤坏死因子受体以及与 Fc 融合的单链 Fv 抗体。然而,在蛋清中,外源表达蛋白的 N-连接糖基上发现了诸如唾液酸和半乳糖等末端糖的不完全添加。这可能会对使用转基因鸡产生不利影响,因为这些末端糖的丢失可能会影响从鸡蛋清中纯化的重组蛋白的功能和稳定性,从而无法将其用于药物用途。为了克服这个问题,我们研究了在大多数蛋清蛋白被分泌的蛋白囊中半乳糖基转移酶(GalT)的活性。在蛋白囊中,β1,4-GalT1 的表达水平较低,且半乳糖转移活性较差。因此,我们推测 GalT1 活性的缺乏可能部分导致了蛋清蛋白的不完全糖基化,并通过逆转录病毒介导的基因转移生成了表达 GalT1 的基因改造鸡。从基因改造鸡的蛋白囊细胞制备的高尔基部分中,检测到显著的 GalT 活性。一系列分析表明,天然蛋清蛋白以及与 Fc 片段融合的外源表达的单链 Fv 抗体的半乳糖基化得到了相当大的改善。我们得出结论,具有基因修饰的 GalT 活性的鸡可能是生产半乳糖基化治疗药物的有吸引力的平台。